Roche presents new data at World Muscle Society (WMS) 2021 highlighting new advances for people living with rare neuromuscular disorders
Basel, 24 September 2021 - Roche (SIX: RO, ROG; OTCQX: RHHBY) today announced data from across its growing neuromuscular portfolio at the World Muscle Society (WMS) Virtual Congress 20 – 24 September 2021. The presentations included additional results from the RAINBOWFISH study, evaluating the efficacy and safety of Evrysdi® (risdiplam) in babies with pre-symptomatic spinal muscular atrophy (SMA) from birth to six weeks of age and data supporting the continued clinical investig ation of gene therapy, SRP-9001, in Duchenne muscular dystrophy (DMD).“These new data for Evrysdi may help extend the potential benefits of th...
Source: Roche Investor Update - September 24, 2021 Category: Pharmaceuticals Source Type: news
Roche presents new data at World Muscle Society (WMS) 2021 highlighting new advances for people living with rare neuromuscular disorders
Basel, 24 September 2021 - Roche (SIX: RO, ROG; OTCQX: RHHBY) today announced data from across its growing neuromuscular portfolio at the World Muscle Society (WMS) Virtual Congress 20 – 24 September 2021. The presentations included additional results from the RAINBOWFISH study, evaluating the efficacy and safety of Evrysdi® (risdiplam) in babies with pre-symptomatic spinal muscular atrophy (SMA) from birth to six weeks of age and data supporting the continued clinical investig ation of gene therapy, SRP-9001, in Duchenne muscular dystrophy (DMD).“These new data for Evrysdi may help extend the potential benefits of th...
Source: Roche Media News - September 24, 2021 Category: Pharmaceuticals Source Type: news
Let's cure MND: JRR Tolkien's great-grandson in plea after brother's death
THE GREAT-grandson of Lord Of The Rings author JRR Tolkien says that his family felt "alone, abandoned and ignored" as his late brother Mike battled motor neurone disease. Royd Tolkien nursed his brother daily for three years until his death in 2015, desperately hoping his care would help restore him. (Source: Daily Express - Health)
Source: Daily Express - Health - September 12, 2021 Category: Consumer Health News Source Type: news
Motor Neurone Disease: 'It's like having a death sentence hanging over your family...'
A FAMILY that has lost six members to an inherited form of motor neurone disease has called for the Government to do more to remove the "death sentence" hanging over them. Cris Hoskin says she felt helpless as her two sons died from MND as a result of a familial gene passed down through the male descendants of her grandfather, who had symptoms of the disease at a time when little was known about it. (Source: Daily Express - Health)
Source: Daily Express - Health - August 22, 2021 Category: Consumer Health News Source Type: news
Motor neurone disease: Brave Jo on the cruel illness that robbed her independence
After leaving university, Jo Knowlton focused on starting a career with the police force, as a "forensic imaging officer". (Source: Daily Express - Health)
Source: Daily Express - Health - August 14, 2021 Category: Consumer Health News Source Type: news
Motor neurone disease: Three early warning signs in the hands to look out for
MOTOR neurone disease is a rare condition that affects around two in every 100,000 people in the UK each year. There are about 5,000 people living with the condition in the UK at any one time. Muscle aches are a common complaint among those in the early stages of the condition, particularly in the hands. (Source: Daily Express - Health)
Source: Daily Express - Health - August 9, 2021 Category: Consumer Health News Source Type: news
Assisted dying: Campaigners renewed hope for change in the law
David Peace intends to travel abroad to end his life before his motor neurone disease deteriorates further. (Source: BBC News | Health | UK Edition)
Source: BBC News | Health | UK Edition - August 2, 2021 Category: Consumer Health News Source Type: news
Data for Roche ’s Evrysdi® (risdiplam) published in New England Journal of Medicine shows significant improvement in survival and motor milestones in babies with Type 1 spinal muscular atrophy (SMA)
Basel, 29 July 2021 – Roche (SIX: RO, ROG; OTCQX: RHHBY) today announced that the New England Journal of Medicine (NEJM) has published data from FIREFISH Part 2, a pivotal global study evaluating the efficacy and safety of Evrysdi® (risdiplam) in babies aged 1-7 months old with symptomatic Type 1 spinal muscular atr ophy (SMA). The study met its primary endpoint with 29% of infants (12/41) sitting without support for at least five seconds* by month 12, a milestone not seen in the natural course of the disease. Safety for Evrysdi in the FIREFISH Part 2 study was consistent with its known safety profile.“Without treatme...
Source: Roche Investor Update - July 29, 2021 Category: Pharmaceuticals Source Type: news
Data for Roche ’s Evrysdi® (risdiplam) published in New England Journal of Medicine shows significant improvement in survival and motor milestones in babies with Type 1 spinal muscular atrophy (SMA)
Basel, 29 July 2021 – Roche (SIX: RO, ROG; OTCQX: RHHBY) today announced that the New England Journal of Medicine (NEJM) has published data from FIREFISH Part 2, a pivotal global study evaluating the efficacy and safety of Evrysdi® (risdiplam) in babies aged 1-7 months old with symptomatic Type 1 spinal muscular atr ophy (SMA). The study met its primary endpoint with 29% of infants (12/41) sitting without support for at least five seconds* by month 12, a milestone not seen in the natural course of the disease. Safety for Evrysdi in the FIREFISH Part 2 study was consistent with its known safety profile.“Without treatme...
Source: Roche Media News - July 29, 2021 Category: Pharmaceuticals Source Type: news
Sunday Express MND campaign: Give us the funds so we CAN cure Motor Neurone Disease
THE Sunday Express is today launching a crusade calling for £50million of Government funding for a "game-changing" Motor Neurone Disease Research Institute. (Source: Daily Express - Health)
Source: Daily Express - Health - July 17, 2021 Category: Consumer Health News Source Type: news
OHIO professor awarded NIH grant to research the motor neuron in relation to aging
(Ohio University) The research will look at the role of the motor neuron, the final neuron that connects the nervous system with the muscle, in health and disease. (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - June 30, 2021 Category: International Medicine & Public Health Source Type: news
Health: Exercise can increase the risk of motor neurone disease, scientists warn
Three large-scale genetic analyses involving people who undertake different habitual levels of exercise were conducted by experts from the University of Sheffield looking for links to motor neurone disease. (Source: the Mail online | Health)
Source: the Mail online | Health - June 11, 2021 Category: Consumer Health News Source Type: news
Scientists link intense exercise with MND risk in some people
Those with a certain genetic makeup more likely to develop motor neurone disease, study confirmsRegular strenuous exercise raises the risk of developing motor neurone disease (MND) in people who are genetically predisposed to the condition, researchers say.Scientists at the University of Sheffield found a causal relationship between high intensity physical activity and the disorder among those already susceptible to the disease.Continue reading... (Source: Guardian Unlimited Science)
Source: Guardian Unlimited Science - June 11, 2021 Category: Science Authors: Ian Sample Science editor Tags: Medical research Motor neurone disease Science Health University of Sheffield Education Source Type: news
Motor neurone disease: Intense exercise increases risk, say scientists
Regular and strenuous exercise can increase the risk of MND in people who are vulnerable, scientists say. (Source: BBC News | Health | UK Edition)
Source: BBC News | Health | UK Edition - June 10, 2021 Category: Consumer Health News Source Type: news
Discovering the Secrets of Motor Neurons with Single Cell Sequencing
Researchers identify new motor neuron subgroups and gain insights into amyotrophic lateral sclerosis (ALS). (Source: The Scientist)
Source: The Scientist - May 5, 2021 Category: Science Tags: Podcasts Source Type: news
