Safety and Efficacy of LX102 Gene Therapy in Patients With Neovascular Age-related Macular Degeneration (nAMD) (VENUS)
Conditions: Neovascular Age-Related Macular Degeneration Interventions: Genetic: LX102 subretinal injection; Biological: Aflibercept intravitreal injection Sponsors: Innostellar Biotherapeutics Co.,Ltd Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 9, 2024 Category: Research Source Type: clinical trials

Genetic Association With Various Severities, Phenotypes and Endotypes of Asthma.
Conditions: Asthma Interventions: Genetic: No intervention Sponsors: Chinese University of Hong Kong Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 9, 2024 Category: Research Source Type: clinical trials

The Effect of GIP, GLP-1 and GLP-2 in Individuals With Genetically Altered Receptor Function
Conditions: Incretin Effect Interventions: Drug: GIP(1-42); Drug: GLP-1; Drug: GLP-2; Other: Placebo Sponsors: University of Copenhagen; Gentofte Hospital, Denmark Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 8, 2024 Category: Research Source Type: clinical trials

Correlation Between Psychological Resilience and Genetic, Inflammatory Indicators
Conditions: Genetic Predisposition to Disease; Environment; Adaptation, Psychological; Inflammation Interventions: Other: no intervention Sponsors: Qianfoshan Hospital Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 5, 2024 Category: Research Source Type: clinical trials

A Clinical Study Evaluating the Safety and Efficacy of SKG0201 Injection in Patients With Spinal Muscular Atrophy Type 1
Conditions: Spinal Muscular Atrophy 1 Interventions: Genetic: SKG0201 Injection Sponsors: Kun Sun Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 4, 2024 Category: Research Source Type: clinical trials

First Patient Implanted in PIERRE IDE Clinical Study of the ThecaFlex DRx System for Administration of Spinraza
LOWELL, Mass., Jan. 3, 2024. Alycone Therapeutics Inc. (Alcyone), a biotechnology company pioneering next-generation precision genetic therapies and precision delivery solutions of therapies for complex neurological conditions, announced the first... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - January 3, 2024 Category: Pharmaceuticals Source Type: clinical trials

Efficacy of Dietary Fiber Supplementation (Soloways) in Patients With Specific Genetic Polymorphisms
Conditions: Obesity Interventions: Dietary Supplement: glucomannan, inulin, and psyllium; Other: placebo Sponsors: S.LAB (SOLOWAYS); Center of New Medical Technologies; Triangel Scientific Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 3, 2024 Category: Research Source Type: clinical trials

The Effect and Mechanism of Gene Variation on Neonatal Hyperbilirubinemia
Conditions: Neonatal Hyperbilirubinemia Interventions: Genetic: Genomic sequencing Sponsors: Sixth Affiliated Hospital, Sun Yat-sen University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 1, 2024 Category: Research Source Type: clinical trials

A Trial of the Safety and Efficacy of Single-Dose Administration of ANB-010 in Subjects With Hemophilia A
Conditions: Hemophilia A Interventions: Genetic: ANB-010, dose 1; Genetic: ANB-010, dose 2; Genetic: ANB-010, dose 3 Sponsors: Biocad Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 29, 2023 Category: Research Source Type: clinical trials

A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia
Conditions: Oculopharyngeal Muscular Dystrophy Interventions: Genetic: BB-301: Dose escalation phase 1b cohort 1; Genetic: BB-301: Dose escalation phase 1b cohort 2; Genetic: BB-301: Dose escalation phase 1b cohort 3; Genetic: BB-301: Dose expansion phase 2a Sponsors: Benitec Biopharma, Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 29, 2023 Category: Research Source Type: clinical trials

Choices About Genetic Testing And Learning Your Risk With Smart Technology
Conditions: Ovarian Cancer; Fallopian Tube Cancer; Peritoneal Cancer; Breast Cancer; Pancreas Cancer; Colorectal Cancer; Endometrial Cancer; Prostate Cancer Interventions: Device: Relational Agent; Other: Clinical Letter Sponsors: Rutgers, The State University of New Jersey Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 28, 2023 Category: Research Source Type: clinical trials

Multicenter Analysis of Genomic and Metabolic Data of Neonatal Genetic Diseases
Conditions: Hereditary Diseases Interventions: Genetic: Genomic sequencing Sponsors: Sixth Affiliated Hospital, Sun Yat-sen University Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 27, 2023 Category: Research Source Type: clinical trials

Association of Peripheral Immune Cells With Antidepressant Treatment Response
Conditions: Depressive Disorder; Genetic Change Interventions: Diagnostic Test: Mental assessments Sponsors: Shanghai Mental Health Center Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 27, 2023 Category: Research Source Type: clinical trials

Probiotics in Mild Alzheimer's Disease
Conditions: Neurodegenerative Diseases; Cognition Disorders in Old Age Interventions: Drug: Probiotic Blend Capsule Sponsors: University of Nicosia; Cyprus Institute of Neurology and Genetics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 25, 2023 Category: Research Source Type: clinical trials

Evaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)
Conditions: Pompe Disease (Late-onset) Interventions: Genetic: CRG003 injection Sponsors: Huashan Hospital Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 21, 2023 Category: Research Source Type: clinical trials