Gene therapy for haemophilia.

CONCLUSIONS: No randomised or quasi-randomised clinical trials of gene therapy for haemophilia were identified. Thus, we are unable to determine the safety and efficacy of gene therapy for haemophilia. Gene therapy for haemophilia is still in its nascent stages and there is a need for well-designed clinical trials to assess the long-term feasibility, success and risks of gene therapy for people with haemophilia. PMID: 27996087 [PubMed - as supplied by publisher]

https://www.ncbi.nlm.nih.gov/pubmed/27996087?dopt=Abstract

Source: Cochrane Database of Systematic Reviews - December 19, 2016 Category: Journals (General) Authors: Sharma A, Easow Mathew M, Sriganesh V, Reiss UM Tags: Cochrane Database Syst Rev Source Type: research