Gene Therapy Promising for Rare Syndrome Gene Therapy Promising for Rare Syndrome
A gene therapy strategy has produced impressive results in patients with Sanfilippo syndrome type A (mucopolysaccharidosis IIIA).Medscape Medical News (Source: Medscape Pediatrics Headlines)
Source: Medscape Pediatrics Headlines - April 23, 2021 Category: Pediatrics Tags: Neurology & Neurosurgery News Source Type: news

OSU, Children ’s start to see fruits of research labor
At long last, successes are piling up. The two Columbus institutions have generated not only revenue, but IPOs, several acquisitions, job-creating startups and an FDA-approved gene therapy that has normally non-effusive scientists using the term cure. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 22, 2021 Category: Biotechnology Authors: Carrie Ghose Source Type: news

Trump email announcement says refusing Covid-19 vaccination is "deranged pseudoscience"
(Natural News) In an email blast sent out to his supporters on Monday, former President Donald Trump bashed those who are just saying no to the experimental Wuhan coronavirus (Covid-19) gene therapy injections being administered under his “Operation Warp Speed” mass vaccination scheme. According to Trump, there is no reason for anyone to skip the... (Source: NaturalNews.com)
Source: NaturalNews.com - April 22, 2021 Category: Consumer Health News Source Type: news

Former GlaxoSmithKline executive launches Montco gene therapy startup with $10M in seed funding
The company has "selectively assembled a syndicate of top-tier investors." (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 20, 2021 Category: Biotechnology Authors: John George Source Type: news

Former Genentech execs — including ex-CEO Ian Clark — jump in with IPO-seeking gene therapy company
The company, with sites in the Bay Area, Philadelphia and London, also counts Genentech and a handful of other local biotechs as its competition. (Source: bizjournals.com Health Care:Physician Practices headlines)
Source: bizjournals.com Health Care:Physician Practices headlines - April 20, 2021 Category: American Health Authors: Ron Leuty Source Type: news

Gene therapy company with operations in KoP files for $100M IPO
The company has raised about $265 million, including $148 million in a Series C round disclosed last month. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - April 19, 2021 Category: Pharmaceuticals Authors: Ron Leuty Source Type: news

Gene therapy shows promise in initial trial for patients with childhood blindness
(University of Pennsylvania School of Medicine) A new gene therapy for one of the most common forms of congenital blindness was safe and improved patients' vision, according to initial data from a clinical trial (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - April 19, 2021 Category: International Medicine & Public Health Source Type: news

Gene therapy company with operations in KoP files for $100M IPO
The company has raised about $265 million, including $148 million in a Series C round disclosed last month. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 19, 2021 Category: Biotechnology Authors: Ron Leuty Source Type: news

Former Genentech execs — including ex-CEO Ian Clark — jump in with IPO-seeking gene therapy company
The company, with sites in the Bay Area, Philadelphia and London, also counts Genentech and a handful of other local biotechs as its competition. (Source: bizjournals.com Health Care:Physician Practices headlines)
Source: bizjournals.com Health Care:Physician Practices headlines - April 17, 2021 Category: American Health Authors: Ron Leuty Source Type: news

Former Genentech execs — including ex-CEO Ian Clark — jump in with IPO-seeking gene therapy company
The company, with sites in the Bay Area, Philadelphia and London, also counts Genentech and a handful of other local biotechs as its competition. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 17, 2021 Category: Biotechnology Authors: Ron Leuty Source Type: news

Juniper Biologics Announces the Appointment of Raman Singh as Chief Executive
Singh to lead Juniper Biologics operations from Singapore and deliver medicines in Oncology, Rare/Orphan Diseases and Gene Therapy SINGAPORE, April 15, 2021 -- (Healthcare Sales & Marketing Network) -- Juniper Biologics, a science-led healthcare compan... Biopharmaceuticals, Personnel Juniper Biologics (Source: HSMN NewsFeed)
Source: HSMN NewsFeed - April 15, 2021 Category: Pharmaceuticals Source Type: news

Activist shareholder continues proxy fight with Peninsula gene therapy company
The investor wants to nominate five people to the company's board; the company has three nominees. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - April 15, 2021 Category: Pharmaceuticals Authors: Ron Leuty Source Type: news

Activist shareholder continues proxy fight with Peninsula gene therapy company
The investor wants to nominate five people to the company's board; the company has three nominees. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 15, 2021 Category: Biotechnology Authors: Ron Leuty Source Type: news

Activist shareholder continues proxy fight with Peninsula gene therapy company
The investor wants to nominate five people to the company's board; the company has three nominees. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - April 14, 2021 Category: Pharmaceuticals Authors: Ron Leuty Source Type: news

Activist shareholder continues proxy fight with Peninsula gene therapy company
The investor wants to nominate five people to the company's board; the company has three nominees. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - April 14, 2021 Category: Biotechnology Authors: Ron Leuty Source Type: news

Alliance for Cancer Gene Therapy Summit 2021 features world renowned cancer researchers advancing so
(Alliance for Cancer Gene Therapy) James P. Allison, PhD, Carl H. June, MD and Siddhartha Mukherjee, MD Keynote April 29 Summit on Advancing Solid Tumor Breakthroughs: Eight additional panels on developing the next generation cancer cell and gene therapies. (Source: EurekAlert! - Cancer)
Source: EurekAlert! - Cancer - April 14, 2021 Category: Cancer & Oncology Source Type: news

Gene therapy shows promise in treating rare eye disease in mice
(eLife) A gene therapy protects eye cells in mice with a rare disorder that causes vision loss, especially when used in combination with other gene therapies, shows a study published today in eLife. (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - April 13, 2021 Category: International Medicine & Public Health Source Type: news

Catalent Biologics Completes Madison Facility Expansion to Double...
Catalent, the leading global provider of advanced delivery technologies, development, and manufacturing solutions for drugs, biologics, cell and gene therapies, and consumer health products, today...(PRWeb April 13, 2021)Read the full story at https://www.prweb.com/releases/catalent_biologics_completes_madison_facility_expansion_to_double_clinical_and_commercial_drug_substance_capacity/prweb17862069.htm (Source: PRWeb: Medical Pharmaceuticals)
Source: PRWeb: Medical Pharmaceuticals - April 13, 2021 Category: Pharmaceuticals Source Type: news

FDA D.I.S.C.O. Burst Edition: FDA approval of ABECMA (idecabtagene vicleucel) the first FDA approved cell-based gene therapy for the treatment of adult patients with relapsed or refractory multiple myeloma
Listen to a soundcast of the March 26, 2021 FDA approval of ABECMA (idacabtagene vicleucel) the first cell-based gene therapy for treatment of adult patients with relapsed or refractory multiple myeloma after four or more prior lines of therapy. (Source: FDA Center for Drug Evaluation and Research - What's New)
Source: FDA Center for Drug Evaluation and Research - What's New - April 9, 2021 Category: Drugs & Pharmacology Authors: FDA Source Type: news

Covid's "third wave" will see mass death among the VACCINATED
(Natural News) There is a “third wave” of the Wuhan coronavirus (Covid-19) barreling our way. And those affected by it will be the “vaccinated” who agreed to get injected with experimental gene therapy cocktails that have forever altered their DNA and made them more susceptible to disease and death. Buried within a report compiled by... (Source: NaturalNews.com)
Source: NaturalNews.com - April 8, 2021 Category: Consumer Health News Source Type: news

Mayo researchers reveal gene therapy path for treating children with rare, fatal genetic disease
A gene therapy strategy developed by Mayo Clinic researchers could offer a potential treatment for a rare and fatal genetic disease that often sickens babies in their first days of life. The disease, propionic acidemia, occurs in 1 in 100,000 live births in the U.S. There is no cure. "As soon as the babies start [...] (Source: News from Mayo Clinic)
Source: News from Mayo Clinic - April 7, 2021 Category: Databases & Libraries Source Type: news

Fauci is a dangerous sociopath who must be held accountable for committing crimes against humanity
(Natural News) Fake doctor Anthony Fauci is now trying to claim credit for the experimental gene therapy injections for the Wuhan coronavirus (Covid-19) that were actually created by Donald Trump through Operation Warp Speed (OWS). Consequently, Fauci is now receiving flack from Trump supporters like Peter Navarro who say that Fauci is nothing more than... (Source: NaturalNews.com)
Source: NaturalNews.com - April 5, 2021 Category: Consumer Health News Source Type: news

$2.1 Million Price Prevents Couple From Buying Life Saving Medication For Their 14 Month Old Daughter
One family is racing against time to treat Ayah, their 14-month-old daughter, who has a rare genetic disease. The gene therapy she... (Source: Reuters: Health)
Source: Reuters: Health - April 2, 2021 Category: Consumer Health News Source Type: news

Researchers devise more efficient, enduring CAR gene therapy to combat HIV
FINDINGSA UCLA research team has shown that using a truncated form of the CD4 molecule as part of a gene therapy to combat HIV yielded superiorand longer-lastingresults in mouse models than previous similar therapies using the CD4 molecule.This new approach to CAR T gene therapy — a type of immunotherapy that involves genetically engineering the body ’s own blood-forming stem cells to create HIV-fighting T cells— has the potential to not only destroy HIV-infected cells but to create “memory cells” that could provide lifelong protection from infection with the virus that causes AIDS.BACKGROUNDC...
Source: UCLA Newsroom: Health Sciences - April 1, 2021 Category: Universities & Medical Training Source Type: news

Researchers devise more efficient, enduring CAR gene therapy to combat HIV
(University of California - Los Angeles Health Sciences) A UCLA research team has shown that using a truncated form of the CD4 molecule as part of a gene therapy to combat HIV yielded superior and longer-lasting results in mouse models than previous similar therapies using the CD4 molecule. (Source: EurekAlert! - Infectious and Emerging Diseases)
Source: EurekAlert! - Infectious and Emerging Diseases - April 1, 2021 Category: Infectious Diseases Source Type: news

First Cell-Based Gene Therapy Approved for Multiple Myeloma
TUESDAY, March 30, 2021 -- Abecma (idecabtagene vicleucel), a chimeric antigen receptor (CAR) T-cell therapy, was approved by the U.S. Food and Drug Administration for the treatment of multiple myeloma, the agency announced Saturday. Abecma, a... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - March 30, 2021 Category: Pharmaceuticals Source Type: news

UC group launches clinical trial using CRISPR to correct sickle cell disease gene defect
Scientists at UCLA, UC San Francisco and UC Berkeley have received U.S. Food and Drug Administration approval to jointly launch an early phase, first-in-human clinical trial of a CRISPR gene correction therapy in patients with sickle cell disease using the patients ’ own blood-forming stem cells.The trial will combine CRISPR technology developed at the Innovative Genomics Institute — a UC Berkeley–UCSF initiative founded by Berkeley’s Nobel Prize–winning scientist Jennifer Doudna — with UCLA’s expertise in genetic analysis and cell manufacturing, and the decades-long expertise at U...
Source: UCLA Newsroom: Health Sciences - March 30, 2021 Category: Universities & Medical Training Source Type: news

< a href= " /news-events/nih-research-matters/gene-therapy-chronic-pain-relief " > Gene therapy for chronic pain relief < /a >
Turning off a particular gene prevented or alleviated chronic pain in mice. The results could lead to an alternative to opioids for treating chronic pain. (Source: NIH Research Matters from the National Institutes of Health (NIH))
Source: NIH Research Matters from the National Institutes of Health (NIH) - March 30, 2021 Category: Consumer Health News Source Type: news

Small Business, Big Mission: Biotech company brings it all together
With early funding from California's Oakland-based stem cell research funding agency for its academic founders, the Stanford University spinout is tapping the CRISPR gene-editing technology out of UC Berkeley to push an experimental gene therapy for sickle cell disease into an early-stage clinical trial and pursue fixes for rare genetic diseases. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - March 26, 2021 Category: Pharmaceuticals Authors: Ron Leuty Source Type: news

After getting caught FAKING vaccine efficacy data, AstraZeneca "revises" its numbers... but it's all still a cruel farce
(Natural News) Following an upswell of criticism, drug giant AstraZeneca has “revised” the efficacy data for its experimental Wuhan coronavirus (Covid-19) gene therapy injection, which has been exposed for triggering deadly blood clots and death in many recipients. After lying about the jab to make the injection appear safe and effective, which it certainly is... (Source: NaturalNews.com)
Source: NaturalNews.com - March 26, 2021 Category: Consumer Health News Source Type: news

VAX COLLAPSE: Vaccine mandates are causing catastrophic logistics failures in international shipping
(Natural News) A new requirement that forces all seafarers to be injected with experimental Wuhan coronavirus (Covid-19) gene therapy cocktails before entering shipping ports is causing major “delays and disruptions” throughout the global supply chain. The International Chamber of Shipping (ICS) says reports are flooding in about entire payloads being denied due to their shipping... (Source: NaturalNews.com)
Source: NaturalNews.com - March 25, 2021 Category: Consumer Health News Source Type: news

Philadelphia gene therapy developer spun out of Temple to raise over $100M via SPAC
The combined company will remain in Philadelphia and accelerate its development of gene therapies. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - March 23, 2021 Category: Biotechnology Authors: John George Source Type: news

New anti-cancer therapy: Converting glioma cells into neurons
(Guangdong-Hongkong-Macau Institute of CNS Regeneration,Jinan University) Glioma is a fatal neurological disorder that has limited interventional treatment, despite extensive research over the past several decades. A research team led by Dr. Gong Chen,has developed a novel gene therapy to reprogram glioma cells into functional neurons, shedding new light on glioma treatment. The work has been published in Cancer Biology& Medicine on March 22, 2021 (Source: EurekAlert! - Cancer)
Source: EurekAlert! - Cancer - March 23, 2021 Category: Cancer & Oncology Source Type: news

G-CON PODs Selected by Matica Biotechnology for GMP Viral Vector...
PODs will support the CDMO’s clinical and commercial production of cell and gene therapies.(PRWeb March 23, 2021)Read the full story at https://www.prweb.com/releases/g_con_pods_selected_by_matica_biotechnology_for_gmp_viral_vector_facility_in_college_station_tx/prweb17812189.htm (Source: PRWeb: Medical Pharmaceuticals)
Source: PRWeb: Medical Pharmaceuticals - March 23, 2021 Category: Pharmaceuticals Source Type: news

Gene Therapy for ALD Prevents Major Functional Disabilities Gene Therapy for ALD Prevents Major Functional Disabilities
Six years after just one gene therapy treatment, physical and neurologic functions have remained largely intact in patients with cerebral adrenoleukodystrophy (ALD).Medscape Medical News (Source: Medscape Neurology and Neurosurgery Headlines)
Source: Medscape Neurology and Neurosurgery Headlines - March 22, 2021 Category: Neurology Tags: Hematology-Oncology News Source Type: news

Catalent Signs Drug Development Agreement with Cybin Inc for its...
Catalent, the leading global provider of advanced delivery technologies, development, and manufacturing solutions for drugs, biologics, cell and gene therapies, and consumer health products, today...(PRWeb March 22, 2021)Read the full story at https://www.prweb.com/releases/catalent_signs_drug_development_agreement_with_cybin_inc_for_its_fast_dissolve_formulation_of_novel_deuterated_tryptamine_cyb003/prweb17810721.htm (Source: PRWeb: Medical Pharmaceuticals)
Source: PRWeb: Medical Pharmaceuticals - March 22, 2021 Category: Pharmaceuticals Source Type: news

'We do not bluff': Peninsula biotech company in showdown with hedge fund
As it takes professional and personal swipes at board members and management of the gene therapy company, an activist investor wants to install five nominees as directors. (Source: bizjournals.com Health Care News Headlines)
Source: bizjournals.com Health Care News Headlines - March 19, 2021 Category: Health Management Authors: Ron Leuty Source Type: news

Gene therapy using 'zinc fingers' may help treat Alzheimer's disease, animal study shows
(Massachusetts General Hospital) A single injection of a gene therapy involving what are called zinc fingers dramatically reduced levels of tau, a protein implicated in Alzheimer's disease, in mice with the condition. The treatment was long lasting, caused no side effects, and reduced Alzheimer's-related damage in the brain. (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - March 19, 2021 Category: International Medicine & Public Health Source Type: news

New cancer-fighting immunotherapy enters clinical trials
(Max Delbr ü ck Center for Molecular Medicine in the Helmholtz Association) Researchers from the MDC and Charit é have developed a new gene therapy based around a special T-cell receptor that helps the immune system effectively recognize and fight cancer cells. The safety of the novel therapy is now being tested on patients with bone marrow cancer in a phase I clinical trial. (Source: EurekAlert! - Cancer)
Source: EurekAlert! - Cancer - March 18, 2021 Category: Cancer & Oncology Source Type: news

Alliance for Cancer Gene Therapy announces Summit 2021 be there when the next breakthroughs happens
(Alliance for Cancer Gene Therapy) Alliance for Cancer Gene Therapy wants to change the C-word from Cancer to Cure. On April 29, 2021, the organization is bringing together world renowned scientists and companies who are driving the latest advances in cancer cell and gene therapy for solid tumors to the Alliance for Cancer Gene Therapy Summit 2021. (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - March 18, 2021 Category: International Medicine & Public Health Source Type: news

Covid-19 mRNA Vaccines Are Not ‘Gene Therapy,’ As Some Are Claiming
Here are the differences between the Pfizer/BioNTech and Moderna Covid-19 vaccines and gene therapy. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - March 18, 2021 Category: Pharmaceuticals Authors: Bruce Y. Lee, Senior Contributor Tags: Healthcare /healthcare Innovation /innovation Science /science business pharma Source Type: news

$81M raise for gene therapy firm in RTP will help double headcount, CEO says
It's another sign of the Triangle's rapid growth in the gene therapy sector. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - March 17, 2021 Category: Biotechnology Authors: David Purtell Source Type: news

$81M raise for gene therapy firm in RTP will help double headcount, CEO says
It's another sign of the Triangle's rapid growth in the gene therapy sector. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - March 17, 2021 Category: Pharmaceuticals Authors: David Purtell Source Type: news

Cellular benefits of gene therapy seen decades after treatment
(University College London) An international collaboration between Great Ormond Street Hospital, the UCL GOS Institute for Child Health and Harvard Medical School has shown that the beneficial effects of gene therapy can be seen decades after the transplanted blood stem cells has been cleared by the body. (Source: EurekAlert! - Medicine and Health)
Source: EurekAlert! - Medicine and Health - March 17, 2021 Category: International Medicine & Public Health Source Type: news

Catalent Expands Partnership with Johnson & Johnson to...
Catalent, the leading global provider of advanced delivery technologies, development, and manufacturing solutions for drugs, biologics, cell and gene therapies, and consumer health products, today...(PRWeb March 17, 2021)Read the full story at https://www.prweb.com/releases/catalent_expands_partnership_with_johnson_johnson_to_significantly_increase_capacity_for_sterile_manufacturing_and_packaging_of_covid_19_vaccine_in_italy/prweb17803353.htm (Source: PRWeb: Medical Pharmaceuticals)
Source: PRWeb: Medical Pharmaceuticals - March 17, 2021 Category: Pharmaceuticals Source Type: news

With one sickle cell drug approved, Peninsula drug maker licenses two more
As potential one-shot-and-done gene therapies beckon for sickle cell disease patients, this South San Francisco pioneer is adding to its portfolio of tablets and pills. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - March 16, 2021 Category: Pharmaceuticals Source Type: news

With one sickle cell drug approved, Peninsula drug maker licenses two more
As potential one-shot-and-done gene therapies beckon for sickle cell disease patients, this South San Francisco pioneer is adding to its portfolio of tablets and pills. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - March 16, 2021 Category: Biotechnology Source Type: news

Accelerated timeline puts spotlight on firm's $80M Durham expansion
A gene therapy company's 200-job expansion in Durham – announced in January – meant a hot start for economic developers in 2021. Now, executives with the firm say their plan for the Durham facility has become even more critical. (Source: bizjournals.com Health Care:Physician Practices headlines)
Source: bizjournals.com Health Care:Physician Practices headlines - March 15, 2021 Category: American Health Authors: Lauren Ohnesorge Source Type: news

Clinical Trial Begins For Gene Therapy To Treat Alzheimer ’s Disease
20 years after their first attempt, UCSD researchers are trying again with a more powerful drug and a more effective delivery method. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - March 12, 2021 Category: Pharmaceuticals Authors: Caroline Seydel, Contributor Tags: Healthcare /healthcare Innovation /innovation Source Type: news

Gene Therapy for Sickle Cell Did Not Cause Patient's Leukemia
THURSDAY, March 11, 2021 -- There is no evidence that a promising gene therapy for sickle cell disease triggered leukemia in a patient, according to the company testing the experimental treatment. Bluebird Bio announced a few weeks ago that a sickle... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - March 11, 2021 Category: Pharmaceuticals Source Type: news