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A breakthrough in gene therapy has allowed a young boy to experience the sensation of sound for the first time in his life. CNN's Danny Freeman reports. (Source: CNN.com - Health)
Source: CNN.com - Health - January 28, 2024 Category: Consumer Health News Source Type: news
A Cure for Hearing Loss? Gene Therapies Are Getting Closer
(Source: Reuters: Health)
Source: Reuters: Health - January 27, 2024 Category: Consumer Health News Source Type: news
Gene therapies that let deaf children hear bring hope —and many questions
The past few months have brought electrifying news that, for the first time, a gene therapy has provided some hearing to children born with mutations that left them deaf. Eli Lilly
announced
this week, for example, that a profoundly deaf boy from Morocco given its treatment as part of a clinical trial in Philadelphia can now hear. And five children in China treated similarly at younger ages gained hearing with some able to verbally communicate without their cochlear implants. Their hearing recovery, first covered by the
press
in October 2023, is described in detail this week in
The Lancet
...
Source: ScienceNOW - January 26, 2024 Category: Science Source Type: news
Novel Gene Therapy Allows Kids With Inherited Deafness to Hear
(MedPage Today) -- A small study published Wednesday documents significantly restored hearing in five of six kids treated in China. On Tuesday, the Children's Hospital of Philadelphia announced similar improvements in an 11-year-old boy treated... (Source: MedPage Today Pediatrics)
Source: MedPage Today Pediatrics - January 25, 2024 Category: Pediatrics Source Type: news
Experimental Gene Therapy Allows Kids with Inherited Deafness to Hear
Gene therapy has allowed several children born with inherited deafness to hear.
A small study published Wednesday documents significantly restored hearing in five of six kids treated in China. On Tuesday, the Children’s Hospital of Philadelphia announced similar improvements in an 11-year-old boy treated there. And earlier this month, Chinese researchers published a study showing much the same in two other children.
[time-brightcove not-tgx=”true”]
So far, the experimental therapies target only one rare condition. But scientists say similar treatments could someday help many mor...
Source: TIME: Health - January 25, 2024 Category: Consumer Health News Authors: LAURA UNGAR/AP Tags: Uncategorized wire Source Type: news
Gene Therapy Brings Hearing to Kids With Congenital Deafness
THURSDAY, Jan. 25, 2024 -- Five of six Chinese children born deaf due to a rare genetic defect now have the ability to hear, thanks to an experimental gene therapy.
The therapy involved a hollowed-out virus loaded with a healthy version of the gene... (Source: Drugs.com - Daily MedNews)
Source: Drugs.com - Daily MedNews - January 25, 2024 Category: General Medicine Source Type: news
Gene therapy shows promise for an inherited form of deafness
For the first time, gene therapy is showing promise for treating inherited deafness, researchers reported Wednesday. A study involving six children born with a genetic defect that left them profoundly deaf found that an experimental form…#zhengyichen #masseye #harvardmedicalschool #boston #lancet #eyeenthospital #fudanuniversity #lawrencelustig #hearing #lustig (Source: Reuters: Health)
Source: Reuters: Health - January 25, 2024 Category: Consumer Health News Source Type: news
Experimental gene therapy allows kids with inherited deafness to hear
Gene therapy has allowed several children born with inherited deafness to hear (Source: ABC News: Health)
Source: ABC News: Health - January 25, 2024 Category: Consumer Health News Tags: Health Source Type: news
White House Pharmacy a Mess; Doctor Dies in Avalanche; Gene Therapy for Deafness
(MedPage Today) -- Note that some links may require registration or subscription.
The White House Medical Unit pharmacy had severe systemic problems including improper recordkeeping, according to an investigation by the Department of Defense Office... (Source: MedPage Today Public Health)
Source: MedPage Today Public Health - January 24, 2024 Category: American Health Source Type: news
Gene Therapy Allows an 11-Year-Old Boy to Hear for the First Time
The genetic treatment targeted a particular kind of congenital deafness and will soon be tried in children who are younger. (Source: NYT Health)
Source: NYT Health - January 23, 2024 Category: Consumer Health News Authors: Gina Kolata Tags: Genetic Engineering Deafness Clinical Trials Children ' s Hospital of Philadelphia Eli Lilly and Company Research Morocco Akouos Inc Dam, Aissam Children and Childhood Source Type: news
Gene Therapy for Sickle Cell Disease Likely Cost-Effective if Under $2 Million
(MedPage Today) -- Compared with common care, gene therapy for sickle cell disease (SCD) would likely be cost-effective if its price was below $2 million, according to a comparative modeling analysis.
At an assumed $2 million price tag for gene... (Source: MedPage Today Public Health)
Source: MedPage Today Public Health - January 22, 2024 Category: American Health Source Type: news
Gene Therapy for Sickle Cell Disease Likely Cost-Effective at
MONDAY, Jan. 22, 2024 -- Gene therapy for sickle cell disease (SCD) below $2 million is likely to be cost-effective, according to a study published online Jan. 23 in the Annals of Internal Medicine.Anirban Basu, Ph.D., from The Comparative Health... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - January 22, 2024 Category: Pharmaceuticals Source Type: news
CRISPR-Based Gene Therapy Earns Beta Thalassemia Approval CRISPR-Based Gene Therapy Earns Beta Thalassemia Approval
Exa-cel earned its second FDA approval. The one-time therapy, which has a list price of $2.2 million in the United States, should be available for patients early this year.Medscape Medical News (Source: Medscape Hematology-Oncology Headlines)
Source: Medscape Hematology-Oncology Headlines - January 17, 2024 Category: Cancer & Oncology Tags: Hematology-Oncology Source Type: news
US FDA approves Vertex/CRISPR gene therapy for an inherited blood disorder
The headquarters of US biopharmaceutical company Vertex Pharmaceuticals in Boston, Massachusets, on November 4, 2023. The U.S. health regulator has approved Vertex Pharmaceuticals and CRISPR Therapeutics' gene therapy to treat a rare blood disorder requiring regular blood transfusions, in patients…#boston #massachusets #crisprtherapeutics #vertex #oppenheimer #hartajsingh (Source: Reuters: Health)
Source: Reuters: Health - January 17, 2024 Category: Consumer Health News Source Type: news
ClearPoint Neuro gets FDA nod for SmartFrame OR Stereotactic System
ClearPoint Neuro, a global device, cell, and gene therapy-enabling company, has received 510(k) clearance from the U.S. Food and Drug Administration (FDA) for its SmartFrame OR stereotactic system for brain and spinal treatment navigation.
The system consists of two main components, SmartFrame OR and ClearPointer Optical Navigation Wand. SmartFrame OR provides stereotactic guidance for the placement and operation of instruments or devices during planning. This includes the operation of neurological procedures performed along with the use of a compatible optical stereotaxic navigation system using preoperative MR and/or CT...
Source: AuntMinnie.com Headlines - January 16, 2024 Category: Radiology Authors: AuntMinnie.com staff writers Tags: Industry News Source Type: news
