Equitable treatment options for pediatric patients with sickle cell disease
Gene therapy, once approved for sickle cell disease, could offer a lifelong cure without the risk associated with allotransplantation. (Source: Yale Science and Health News)
Source: Yale Science and Health News - December 8, 2023 Category: Universities & Medical Training Source Type: news

Milestone Gene Therapies for Sickle Cell Disease Greenlit by FDA
(MedPage Today) -- The FDA approved two cell-based gene therapies, exagamglogene autotemcel (Casgevy) and lovotibeglogene autotemcel (Lyfgenia), for sickle cell disease (SCD), the agency announced. Marking the first FDA-approved therapy utilizing... (Source: MedPage Today Public Health)
Source: MedPage Today Public Health - December 8, 2023 Category: American Health Source Type: news

University of Maryland Scientists Image World ’s First ‘Vampire Virus’
Research could lead to improvements in gene therapy and antiviral resistance medications while also possibly leading to a new class of clinical laboratory tests Scientists at the University of Maryland, Baltimore County (UMBC) have discovered what may be the scariest virus of all—the Vampire Virus. It’s a term that may inspire “Walking Dead” level horror […] The post University of Maryland Scientists Image World’s First ‘Vampire Virus’ appeared first on Dark Daily. (Source: Dark Daily)
Source: Dark Daily - December 8, 2023 Category: Laboratory Medicine Authors: Jillia Schlingman Tags: Digital Pathology Laboratory Instruments & Laboratory Equipment Laboratory News Laboratory Resources Laboratory Testing anatomic pathology antiviral drug resistance antiviral medication bioinformatics capsid clinical laboratory clini Source Type: news

Voyager Therapeutics Announces Selection of Development Candidate for SOD1 Amyotrophic Lateral Sclerosis Gene Therapy Program
LEXINGTON, Mass., Dec. 06, 2023 (GLOBE NEWSWIRE) -- Voyager Therapeutics, Inc. VYGR, a biotechnology company dedicated to breaking through barriers in gene therapy and neurology, today announced that it has selected a lead development candidate for its superoxide dismutase 1 (SOD1)-mutated…#lexington #mass #als #voyager #sod1 #iv #tracer #voyagersod1als #g93a #alfredwsandrock (Source: Reuters: Health)
Source: Reuters: Health - December 6, 2023 Category: Consumer Health News Source Type: news

Genetic Testing Warranted in Epilepsy of Unknown Origin Genetic Testing Warranted in Epilepsy of Unknown Origin
Benefits of genetic testing in adults with unexplained epilepsy include enrollment in a clinical trial of a relevant gene therapy, connection to families with a similar diagnosis, and peace of mind.Medscape Medical News (Source: Medscape Neurology and Neurosurgery Headlines)
Source: Medscape Neurology and Neurosurgery Headlines - December 5, 2023 Category: Neurology Tags: Neurology & Neurosurgery Source Type: news

Rocket Pharma Seeks Gene Therapy Revolution For Genetic Heart Disease
Rocket Pharma has a pipeline of six gene therapy programs addressing cardiovascular and hematology-based diseases at the genetic level. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - December 5, 2023 Category: Pharmaceuticals Authors: Yola Robert, Senior Contributor Tags: ForbesWomen /forbeswomen Leadership /leadership Innovation /innovation Healthcare /healthcare standard Source Type: news

Durham biotech seeks partner to advance its gene therapy
Atsena Therapeutics is looking for a partner to advance one of its gene therapy programs targeting blindness. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - December 4, 2023 Category: Biotechnology Authors: Zac Ezzone Source Type: news

First Gene Therapy for Non-Muscle-Invasive Bladder Cancer Offers Durable Response
(MedPage Today) -- WASHINGTON -- The gene therapy nadofaragene firadenovec (Adstiladrin) continued to demonstrate clinical activity in patients with high-risk bladder cancer, researchers reported. The long-term follow-up data came from a phase... (Source: MedPage Today Hematology/Oncology)
Source: MedPage Today Hematology/Oncology - December 4, 2023 Category: Hematology Source Type: news

Xtalks Announces its Life Science Webinar Calendar for December 2023
Upcoming free, educational webinars from Xtalks will feature topics on cell and gene therapy, clinical trials, commercialization & HEOR, drug discovery & development, fundamental research, healthcare, laboratory technology, medical device, patient recruitment & retention, pharma... (Source: PRWeb: Medical Pharmaceuticals)
Source: PRWeb: Medical Pharmaceuticals - December 4, 2023 Category: Pharmaceuticals Tags: FVT TRI Source Type: news

Why ‘ Healthspan ’ May Be More Important Than Lifespan
In 2014, then-57-year-old bioethicist Dr. Ezekiel Emanuel wrote an infamous essay titled, “Why I Hope to Die at 75” for The Atlantic. His argument boiled down to this: it’s not worth living as long as humanly possible if those efforts yield extra decades defined by disease and poor health, which data suggest is the fate awaiting many people in the U.S. Nearly a decade later, neither Emanuel’s mind nor the statistics have changed much. Emanuel still says he plans to stop most life-extending medical care once he reaches age 75, though he’s healthy enough that he expects to live longer natural...
Source: TIME: Health - November 30, 2023 Category: Consumer Health News Authors: Jamie Ducharme Tags: Uncategorized healthscienceclimate Source Type: news

Moderna-partnered gene therapy firm to lay off 68, including two execs
An Atlas Venture-backed startup developing gene therapies is laying off nearly half of its workforce. (Source: bizjournals.com Health Care:Biotechnology headlines)
Source: bizjournals.com Health Care:Biotechnology headlines - November 29, 2023 Category: Biotechnology Authors: Rowan Walrath Source Type: news

AmplifyBio expands capabilities – and rentable lab space – in New Albany facility
The massive 350,000-square-foot facility also could ease Central Ohio's space crunch for biotech startups such as gene therapy spinouts from Nationwide Children's Hospital and Ohio State University (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - November 28, 2023 Category: Pharmaceuticals Authors: Carrie Ghose Source Type: news

Key Data on Macular Degeneration From AAO 2023 Key Data on Macular Degeneration From AAO 2023
Key data on treatment of macular degeneration, from AAO 2023, include extended study results on pegcetacoplan and avacincaptad pegol, as well as findings in gene therapy, as reported by Dr Sunir Garg.Medscape (Source: Medscape Today Headlines)
Source: Medscape Today Headlines - November 28, 2023 Category: Consumer Health News Tags: None ReCAP Source Type: news

UK Approves Groundbreaking CRISPR-Based Gene Therapy For Sickle Cell Disease And Thalassemia
Gene therapy takes a giant leap forward as Exa-cel becomes the world ’s first CRISPR/Cas9 gene-edited therapy approved to treat sickle cell disease and thalassemia. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - November 18, 2023 Category: Pharmaceuticals Authors: William A. Haseltine, Contributor Tags: Healthcare /healthcare Innovation /innovation business pharma & standard Source Type: news

UK approves gene therapy to cure two blood disorders - BBC News
(Source: Reuters: Health)
Source: Reuters: Health - November 18, 2023 Category: Consumer Health News Source Type: news