Valoctocogene Roxaparvovec and Etranacogene Dezaparavovec: Novel Gene Therapies for Hemophilia A and B

CONCLUSION: Valoctocogene and etranacogene provide another treatment for selected patients with hemophilia. Treatment for the patient with hemophilia (gene therapy vs replacement strategy) must be personalized as new clinical data are published being cognizant of drug affordability.PMID:37978816 | DOI:10.1177/10600280231202247

Source: The Annals of Pharmacotherapy - November 18, 2023 Category: Drugs & Pharmacology Authors: John A Dougherty Kristiann M Dougherty Source Type: research