First gene-editing therapy could win FDA approval to treat sickle cell disease - crippling condition that leaves sufferers in life-altering pain
A US FDA advisory committee announced it would consider approving the gene-editing drug Casgevy to treat sickle cell disease, which affects 100,000 Americans. It has been approved in the UK. (Source: the Mail online | Health)
Source: the Mail online | Health - November 17, 2023 Category: Consumer Health News Source Type: news
Crispr Therapeutics (NASDAQ:CRSP) Notches Up on World-First Therapy - TipRanks.com
Great news emerged out of biotech stock Crispr Therapeutics (NASDAQ:CRSP), particularly for those who suffer from sickle-cell anemia. A new treatment for the disease was created using the genetic modification tool, and it’s given Crispr stock a boost, up nearly 5% in Tuesday morning’s trading…#crisprtherapeutics #unitedkingdom #exacel #samarthkulkarni #moderatebuy #crsp #holds (Source: Reuters: Health)
Source: Reuters: Health - November 17, 2023 Category: Consumer Health News Source Type: news
Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval
The first treatment that relies on CRISPR is expected to receive U.S. approval next month. But it may cost millions of dollars per patient. (Source: NYT Health)
Source: NYT Health - November 17, 2023 Category: Consumer Health News Authors: Gina Kolata Tags: Sickle Cell Anemia Genetics and Heredity Genetic Engineering Blood Bone Marrow Hemoglobin Crispr (DNA) Drugs (Pharmaceuticals) CRISPR Therapeutics Vertex Pharmaceuticals Inc Source Type: news
The world's first gene therapy for sickle cell disease has been approved in the UK
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement Thursday, the Medicines and Healthcare Regulatory Agency said it approved…#nobel #crisprtherapeutics #crispr #mhra #african #caribbean #southasian #southeastasian #middleeastern #jameslabelle (Source: Reuters: Health)
Source: Reuters: Health - November 16, 2023 Category: Consumer Health News Source Type: news
UK becomes first country to approve Crispr gene-editing therapy
The UK has become the first country to approve a therapy based on Crispr gene editing, with the regulator authorizing a treatment for sickle cell disease and beta thalassemia. The Medicines and Healthcare products Regulatory Agency has approved the therapy, called Casgevy, which was developed by…#healthcare #crisprtherapeutics #jenniferdoudna #anobelprize #budget #jeremyhunt #julianbeach #mhra #financialtimesltd (Source: Reuters: Health)
Source: Reuters: Health - November 16, 2023 Category: Consumer Health News Source Type: news
The world's first gene therapy for sickle cell disease has been approved in Britain
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling illness in the U.K. In a statement on Thursday, the Medicines and... (Source: ABC News: Health)
Source: ABC News: Health - November 16, 2023 Category: Consumer Health News Tags: Health Source Type: news
World-first gene therapy for 2 blood disorders — sickle cell and thalassemia — approved
Britain's medical regulator has announced it's authorized a gene therapy for sickle-cell disease and another type of inherited blood disorder for patients aged 12 and over. (Source: CBC | Health)
Source: CBC | Health - November 16, 2023 Category: Consumer Health News Tags: News/Health Source Type: news
CRISPR Therapy Gets U.K. Approval, the First in the World
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K.
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In a statement on Thursday, the Medicines and Healthcare Regulatory Agency said it approved Casgevy, the first medicine licensed using the gene editing tool CRISPR, which won its makers a Nobel prize in 2020.
The agency approved the treatment for patients with sickle cell disease and thalassemia who are 12 years old and over. Casgevy is made by Vertex ...
Source: TIME: Health - November 16, 2023 Category: Consumer Health News Authors: MARIA CHENG / AP Tags: Uncategorized Drugs wire Source Type: news
UK medicines regulator approves gene therapy for two blood disorders
MHRA authorises uses of Casgevy as a potential cure for sickle cell disease and beta thalassemiaBritain ’s drugs regulator has approved a groundbreaking treatment for two painful and debilitating lifelong blood disorders, which works by “editing” the gene that causes them.The Medicines and Healthcare products Regulatory Agency (MHRA) has given thegreen light for Casgevy to be used to treatsickle cell disease andbeta thalassemia.Continue reading... (Source: Guardian Unlimited Science)
Source: Guardian Unlimited Science - November 16, 2023 Category: Science Authors: Denis Campbell Health policy editor Tags: Gene editing Medical research Sickle cell disease NHS Health Society UK news Regulators Science Genetics Pharmaceuticals industry Business Source Type: news
UK becomes 1st country to approve gene therapy treatment for sickle cell, thalassemia
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement on Thursday, the Medicines and... (Source: ABC News: Health)
Source: ABC News: Health - November 16, 2023 Category: Consumer Health News Tags: Health Source Type: news
U.K. Greenlights World ’s First Crispr Gene Editing Therapy
The treatment, authorized for sickle cell disease and beta thalassemia, is being considered for approval by the FDA, with a decision expected in December. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - November 16, 2023 Category: Pharmaceuticals Authors: Robert Hart, Forbes Staff Tags: Business /business Innovation /innovation Science /science Healthcare /healthcare Breaking breaking-news topline Source Type: news
UK approves Crispr gene editing therapy in global first
Regulator authorises treatment for sickle cell disease and beta thalassaemia (Source: FT.com - Drugs and Healthcare)
Source: FT.com - Drugs and Healthcare - November 16, 2023 Category: Pharmaceuticals Source Type: news
Casgevy: UK approves gene-editing drug for sickle cell
Medical regulators approve a gene therapy that aims to cure sickle cell disease and beta thalassemia. (Source: BBC News | Health | UK Edition)
Source: BBC News | Health | UK Edition - November 16, 2023 Category: Consumer Health News Source Type: news
Biden ’s Race Against a Cure
The Food and Drug Administration may soon approve two gene therapies with the potential to cure more than 100,000 Americans with debilitating sickle-cell disease. Now the bad news: The Centers for Medicare and Medicaid Services (CMS) may soon limit access to such breakthrough treatments. Gene…#centersformedicare #medicaidservices #cms #fda (Source: Reuters: Health)
Source: Reuters: Health - November 14, 2023 Category: Consumer Health News Source Type: news
AAO: Research Highlights Vision Issues Seen in Pediatric Sickle Cell Disease
THURSDAY, Nov. 9, 2023 -- For pediatric patients with sickle cell disease (SCD), ophthalmologic complications include nonproliferative retinopathy (NPR) and proliferative retinopathy (PR), which occur in 33 and 6 percent, respectively, according to... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - November 9, 2023 Category: Pharmaceuticals Source Type: news
