First CRISPR Sickle Cell Patient ‘Reborn’: FDA Approval Expected
FDA soon rules if gene-editing CRISPR drug Exa-cel can be used commercially to treat sickle cell disease, opening door to many other therapies. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - December 5, 2023 Category: Pharmaceuticals Authors: Ellen Matloff, Contributor Tags: Healthcare /healthcare Innovation /innovation Editors' Pick editors-pick business pharma & standard Source Type: news
ASH 2023: Equity, Sickle Cell, and Real-Life Outcomes ASH 2023: Equity, Sickle Cell, and Real-Life Outcomes
Health equity, sickle cell disease, and the thoughtful use of artificial intelligence and social media are among the key themes to be presented at the annual meeting of the American Society of Hematology.MDedge News (Source: Medscape Hematology-Oncology Headlines)
Source: Medscape Hematology-Oncology Headlines - December 5, 2023 Category: Cancer & Oncology Tags: Hematology-Oncology News Source Type: news
Disease-Modifying Therapy Use for Sickle Cell Remained Low 2014 to 2021
MONDAY, Nov. 27, 2023 -- From 2014 to 2021, uptake of disease-modifying treatments (DMTs) for sickle cell disease (SCD) remained low, according to a study published online Nov. 22 in JAMA Network Open.
Terri Victoria Newman, Pharm.D., from the... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - November 27, 2023 Category: Pharmaceuticals Source Type: news
Medicines for four rare diseases become cheaper due to domestic production
Drugs for four of these diseases -Tyrosinemia Type 1, Gaucher's Disease, Wilson's Disease and Dravet-Lennox Gastaut Syndrome - along with sickle cell Anemia have been approved and are being manufactured indigenously. (Source: The Economic Times Healthcare and Biotech News)
Source: The Economic Times Healthcare and Biotech News - November 25, 2023 Category: Pharmaceuticals Source Type: news
Sickle cell report highlights ‘insufficient’ community nursing support
Community nursing and nurse counselling are the areas suffering most from an overall lack of specialist sickle cell nurses, a new report has found. The Sickle Cell Society’s latest investigation into workforce shortages – called The difference between life and death – said there was an ‘overwhelming consensus’ among healthcare professionals that numbers of specialist... Read moreThe post Sickle cell report highlights ‘insufficient’ community nursing support appeared first on Nursing in Practice. (Source: Nursing in Practice)
Source: Nursing in Practice - November 24, 2023 Category: Nursing Authors: Megan Ford Tags: Community nursing Latest news Source Type: news
EXCLUSIVE: Woman, 21, needs a life-saving blood transfusion after vaping ONCE caused 'acute chest syndrome'
The woman, who was from India, started to suffer pain in her back and ribs shortly after using the vape. She suffered from sickle cell anemia, which raises the risk of complications with vapes. (Source: the Mail online | Health)
Source: the Mail online | Health - November 23, 2023 Category: Consumer Health News Source Type: news
UK Approves Groundbreaking CRISPR-Based Gene Therapy For Sickle Cell Disease And Thalassemia
Gene therapy takes a giant leap forward as Exa-cel becomes the world ’s first CRISPR/Cas9 gene-edited therapy approved to treat sickle cell disease and thalassemia. (Source: Forbes.com Healthcare News)
Source: Forbes.com Healthcare News - November 18, 2023 Category: Pharmaceuticals Authors: William A. Haseltine, Contributor Tags: Healthcare /healthcare Innovation /innovation business pharma & standard Source Type: news
UK Authorizes Gene Therapy for Blood Disorders in World First UK Authorizes Gene Therapy for Blood Disorders in World First
Britain has authorized a gene therapy that aims to cure sickle-cell disease and another type of inherited blood disorder for patients aged 12 and over, the country ' s medical regulator said.Reuters Health Information (Source: Medscape Transplantation Headlines)
Source: Medscape Transplantation Headlines - November 18, 2023 Category: Transplant Surgery Tags: Hematology-Oncology News Source Type: news
Opioid Doc Sentenced; World's First Sickle Cell Gene Tx; FTC Warns Diet Influencers
(MedPage Today) -- Note that some links may require registration or subscription.
A Houston physician was sentenced to 10 years in prison for his role in a $5 million pill-mill scheme, according to the Department of Justice.
In a world first... (Source: MedPage Today Psychiatry)
Source: MedPage Today Psychiatry - November 17, 2023 Category: Psychiatry Source Type: news
First gene-editing therapy could win FDA approval to treat sickle cell disease - crippling condition that leaves sufferers in life-altering pain
A US FDA advisory committee announced it would consider approving the gene-editing drug Casgevy to treat sickle cell disease, which affects 100,000 Americans. It has been approved in the UK. (Source: the Mail online | Health)
Source: the Mail online | Health - November 17, 2023 Category: Consumer Health News Source Type: news
Crispr Therapeutics (NASDAQ:CRSP) Notches Up on World-First Therapy - TipRanks.com
Great news emerged out of biotech stock Crispr Therapeutics (NASDAQ:CRSP), particularly for those who suffer from sickle-cell anemia. A new treatment for the disease was created using the genetic modification tool, and it’s given Crispr stock a boost, up nearly 5% in Tuesday morning’s trading…#crisprtherapeutics #unitedkingdom #exacel #samarthkulkarni #moderatebuy #crsp #holds (Source: Reuters: Health)
Source: Reuters: Health - November 17, 2023 Category: Consumer Health News Source Type: news
Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval
The first treatment that relies on CRISPR is expected to receive U.S. approval next month. But it may cost millions of dollars per patient. (Source: NYT Health)
Source: NYT Health - November 17, 2023 Category: Consumer Health News Authors: Gina Kolata Tags: Sickle Cell Anemia Genetics and Heredity Genetic Engineering Blood Bone Marrow Hemoglobin Crispr (DNA) Drugs (Pharmaceuticals) CRISPR Therapeutics Vertex Pharmaceuticals Inc Source Type: news
The world's first gene therapy for sickle cell disease has been approved in the UK
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling disease in the U.K. In a statement Thursday, the Medicines and Healthcare Regulatory Agency said it approved…#nobel #crisprtherapeutics #crispr #mhra #african #caribbean #southasian #southeastasian #middleeastern #jameslabelle (Source: Reuters: Health)
Source: Reuters: Health - November 16, 2023 Category: Consumer Health News Source Type: news
UK becomes first country to approve Crispr gene-editing therapy
The UK has become the first country to approve a therapy based on Crispr gene editing, with the regulator authorizing a treatment for sickle cell disease and beta thalassemia. The Medicines and Healthcare products Regulatory Agency has approved the therapy, called Casgevy, which was developed by…#healthcare #crisprtherapeutics #jenniferdoudna #anobelprize #budget #jeremyhunt #julianbeach #mhra #financialtimesltd (Source: Reuters: Health)
Source: Reuters: Health - November 16, 2023 Category: Consumer Health News Source Type: news
The world's first gene therapy for sickle cell disease has been approved in Britain
Britain’s medicines regulator has authorized the world’s first gene therapy treatment for sickle cell disease, in a move that could offer relief to thousands of people with the crippling illness in the U.K. In a statement on Thursday, the Medicines and... (Source: ABC News: Health)
Source: ABC News: Health - November 16, 2023 Category: Consumer Health News Tags: Health Source Type: news
