Experimental Gene Therapy Allows Kids with Inherited Deafness to Hear
Gene therapy has allowed several children born with inherited deafness to hear.
A small study published Wednesday documents significantly restored hearing in five of six kids treated in China. On Tuesday, the Children’s Hospital of Philadelphia announced similar improvements in an 11-year-old boy treated there. And earlier this month, Chinese researchers published a study showing much the same in two other children.
[time-brightcove not-tgx=”true”]
So far, the experimental therapies target only one rare condition. But scientists say similar treatments could someday help many mor...
Source: TIME: Health - January 25, 2024 Category: Consumer Health News Authors: LAURA UNGAR/AP Tags: Uncategorized wire Source Type: news
Gene Therapy for Sickle Cell Disease Likely Cost-Effective if Under $2 Million
(MedPage Today) -- Compared with common care, gene therapy for sickle cell disease (SCD) would likely be cost-effective if its price was below $2 million, according to a comparative modeling analysis.
At an assumed $2 million price tag for gene... (Source: MedPage Today Public Health)
Source: MedPage Today Public Health - January 22, 2024 Category: American Health Source Type: news
Gene Therapy for Sickle Cell Disease Likely Cost-Effective at
MONDAY, Jan. 22, 2024 -- Gene therapy for sickle cell disease (SCD) below $2 million is likely to be cost-effective, according to a study published online Jan. 23 in the Annals of Internal Medicine.Anirban Basu, Ph.D., from The Comparative Health... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - January 22, 2024 Category: Pharmaceuticals Source Type: news
COVID-19 Vaccine Uptake Lagging in Patients With Sickle Cell Disease
FRIDAY, Jan. 19, 2024 -- COVID-19 immunization completion is nearly half for people with versus without sickle cell disease (SCD), according to a research letter published online Jan. 8 in JAMA Network Open.
Hannah K. Peng, from the University... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - January 19, 2024 Category: Pharmaceuticals Source Type: news
FDA Approves Casgevy to Treat Beta-Thalassemia
WEDNESDAY, Jan. 17, 2024 -- After approving Casgevy (exagamglogene autotemcel) in December to treat sickle cell disease, the U.S. Food and Drug Administration announced Tuesday that the therapy has now been approved to treat patients older than 12... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - January 17, 2024 Category: Pharmaceuticals Source Type: news
FDA Clears Sickle Cell Drug, Casgevy, to Treat Transfusion-Dependent Beta-Thalassemia
WEDNESDAY, Jan. 17, 2024 -- Casgevy, a groundbreaking treatment that was approved to treat sickle cell disease in December, was given the U.S. Food and Drug Administration ' s blessing on Tuesday to treat another inherited blood disorder.
Casgevy is... (Source: Drugs.com - Daily MedNews)
Source: Drugs.com - Daily MedNews - January 17, 2024 Category: General Medicine Source Type: news
FDA Clears Sickle Cell Drug to Treat Another Blood Disorder
WEDNESDAY, Jan. 17, 2024 -- Casgevy, a groundbreaking treatment that was approved to treat sickle cell disease in December, was given the U.S. Food and Drug Administration ' s blessing on Tuesday to treat another inherited blood disorder.Casgevy is... (Source: Drugs.com - Daily MedNews)
Source: Drugs.com - Daily MedNews - January 17, 2024 Category: General Medicine Source Type: news
Vertex ’s CRISPR drug notches 2nd FDA approval for another rare disease
Just last month, the Boston drugmaker and its partner, CRISPR Therapeutics, earned approval to market the same drug to treat sickle cell disease. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - January 16, 2024 Category: Pharmaceuticals Authors: Hannah Green Source Type: news
COVID Can Threaten Sickle Cell Patients, But Too Few Are Vaccinated
FRIDAY, Jan. 12, 2024 -- Sickle cell disease is one of many chronic health conditions that dramatically increases the risk of hospitalization and death in people infected by COVID-19.Unfortunately, folks with sickle cell disease are much less... (Source: Drugs.com - Daily MedNews)
Source: Drugs.com - Daily MedNews - January 12, 2024 Category: General Medicine Source Type: news
Study: Sickle cell disorder patients less likely to get full COVID-19 vaccine dosage
The recent findings by the University of Michigan ' s academic medical center suggests adults with sickle cell disease are half as likely to have received an initial COVID-19 vaccine dose as people without sickle cell. (Source: Health News - UPI.com)
Source: Health News - UPI.com - January 10, 2024 Category: Consumer Health News Source Type: news
Vertex, bluebird detail rollout plans for competing sickle-cell gene therapies
Vertex and bluebird bio, the companies behind the competing sickle-cell treatments approved in December, have provided new details in their plans to bring the treatments to patients in 2024. (Source: bizjournals.com Health Care:Pharmaceuticals headlines)
Source: bizjournals.com Health Care:Pharmaceuticals headlines - January 8, 2024 Category: Pharmaceuticals Authors: Hannah Green Source Type: news
Focus shifts to healthcare delivery in 2023 as Covid stress eases
A major initiative this year has been the launch of the National Sickle Cell Anaemia Elimination Mission by Prime Minister Narendra Modi in July. The mission is aimed at elimination of the disease in India, particularly among the country's tribal populations in 17 high prevalence states by 2047. (Source: The Economic Times)
Source: The Economic Times - December 31, 2023 Category: Consumer Health News Source Type: news
Monthly News Roundup - December 2023
Landmark FDA Approval for Casgevy, a CRISPR-Based Therapy for Sickle Cell Disease
This past month the U.S. Food and Drug Administration (FDA) cleared Casgevy (exagamglogene autotemcel), the first approved CRISPR/Cas9 genome-edited cell... (Source: Drugs.com - Pharma News)
Source: Drugs.com - Pharma News - December 31, 2023 Category: Pharmaceuticals Source Type: news
13 Ways the World Got Better in 2023
As in most years, much of the media focus in 2023 was on the myriad crises people all over the world faced, from horrific wars in Eastern Europe and the Middle East to devastating natural disasters (many climate-change-related) in Turkey, Southeast Africa, Hawaii, Canada, and more. At the end of this long year, though, it’s worth taking a step back and considering some of the ways things improved. Here are some examples, gathered together by TIME’s climate and health journalists:
[time-brightcove not-tgx=”true”]
COVID-19 death numbers plummeted…
Since the pandemic began, COVID-19 has b...
Source: TIME: Health - December 26, 2023 Category: Consumer Health News Authors: TIME Staff Tags: Uncategorized climate change Climate Is Everything feature healthscienceclimate Source Type: news
The Age of Crispr Medicine Is Here
“The pain is far and away the worst part for patients,” says Alexis Thompson, a sickle cell expert and chief of the Division of Hematology at Children’s Hospital of Philadelphia. “They suffer from really debilitating pain.” Over time, sickle cell damages organs and leads to early death. On…#alexisthompson #crisprtherapeutics #switzerland #boston #janetwatson #watchthem #hiddenoceansnewer #broadinstitute #antarctic #azar (Source: Reuters: Health)
Source: Reuters: Health - December 26, 2023 Category: Consumer Health News Source Type: news
