Niemann-Pick Disease Clinical Trials 
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This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.Orphazyme to Prepare for Filing of Arimoclomol in US for Niemann-Pick Disease Type C (NPC)
Copenhagen, July 21, 2019– Orphazyme A/S (ticker: ORPHA.CO), a biopharmaceutical company dedicated to developing treatments for patients living with rare diseases, today announces that it has had a positive meeting with the FDA and... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - July 21, 2019 Category: Pharmaceuticals Source Type: clinical trials
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials
Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials
