Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition:   Niemann-Pick Disease, Type C1 Intervention:   Drug: VTS-270 Sponsor:   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 25, 2019 Category: Research Source Type: clinical trials

Induced Pluripotent Stem Cells for Niemann Pick Disease
Condition:   Niemann-Pick Diseases Intervention:   Sponsor:   Centogene AG Rostock Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 21, 2019 Category: Research Source Type: clinical trials