Niemann-Pick Disease Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
Open-label Study of VTS-270 in Participants With Neurologic Manifestations of Niemann-Pick Type C1
Condition: Niemann-Pick Disease, Type C Intervention: Drug: VTS-270 Sponsor: Vtesse, Inc., a Mallinckrodt Pharmaceuticals Company Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 19, 2019 Category: Research Source Type: clinical trials
N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)
Condition: Niemann-Pick Disease, Type C Intervention: Drug: IB1001 Sponsor: IntraBio Inc Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 30, 2018 Category: Research Source Type: clinical trials