Open-label Study of VTS-270 in Participants With Neurologic Manifestations of Niemann-Pick Type C1
Condition:   Niemann-Pick Disease, Type C Intervention:   Drug: VTS-270 Sponsor:   Vtesse, Inc., a Mallinckrodt Pharmaceuticals Company Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 19, 2019 Category: Research Source Type: clinical trials

N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)
Condition:   Niemann-Pick Disease, Type C Intervention:   Drug: IB1001 Sponsor:   IntraBio Inc Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 30, 2018 Category: Research Source Type: clinical trials