Niemann-Pick Disease Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.

Orphazyme Completes Enrolment of Patients for Phase 3 Clinical Trial of Arimoclomol in Niemann-pick Type C Disease
May 15, 2017 -- Orphazyme ApS, a Danish biotech company developing novel therapies for the treatment of protein misfolding diseases, today announced the completion of enrolment for its lead program within Niemann-Pick type C disease. Niemann-Pick... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - May 15, 2017 Category: Pharmaceuticals Source Type: clinical trials

Study of the Pharmacokinetics of Trappsol and Effects on Potential Biomarkers of Niemann-Pick C1 (NPC1)
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: Hydroxypropyl-beta-cyclodextrin Sponsor: CTD Holdings, Inc. Not yet recruiting - verified October 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 21, 2016 Category: Research Source Type: clinical trials

Study of Pharmacokinetics and Preliminary Efficacy in Patients With Niemann-Pick C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: Hydroxypropyl-beta-cyclodextrin Sponsor: CTD Holdings, Inc. Not yet recruiting - verified September 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 19, 2016 Category: Research Source Type: clinical trials