A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C
Condition:   Niemann-Pick Disease, Type CIntervention:   Sponsor:   OrphazymeNot yet recruiting - verified April 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 22, 2015 Category: Research Source Type: clinical trials

Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1
Condition:   Neimann-Pick DiseaseIntervention:   Drug: VorinostatSponsors:   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD);   Washington University School of Medicine;   Weill Medical College of Cornell UniversityRecruiting - verified January 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 25, 2014 Category: Research Source Type: clinical trials

Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Condition:   Niemann-Pick Disease, Type C1Intervention:   Drug: 2-hydroxypropyl-beta-cyclodextrinSponsor:   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Recruiting - verified July 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 8, 2012 Category: Research Source Type: clinical trials