Niemann-Pick Disease Clinical Trials This is an RSS file. You can use it to subscribe to this data in your favourite RSS reader or to display this data on your own website or blog.
A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C
Condition: Niemann-Pick Disease, Type CIntervention: Sponsor: OrphazymeNot yet recruiting - verified April 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 22, 2015 Category: Research Source Type: clinical trials
Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1
Condition: Neimann-Pick DiseaseIntervention: Drug: VorinostatSponsors: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Washington University School of Medicine; Weill Medical College of Cornell UniversityRecruiting - verified January 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 25, 2014 Category: Research Source Type: clinical trials
Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Condition: Niemann-Pick Disease, Type C1Intervention: Drug: 2-hydroxypropyl-beta-cyclodextrinSponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Recruiting - verified July 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 8, 2012 Category: Research Source Type: clinical trials