Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1

Condition:   Niemann-Pick Disease, Type C1 Intervention:   Drug: VTS-270 Sponsor:   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials