Combined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Niemann-Pick Disease, Type C1
Condition: Niemann-Pick Disease, Type C1 Intervention: Drug: VTS-270 Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials
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