Fusion of Rabies Virus Glycoprotein or gh625 to Iduronate-2-Sulfatase for the Treatment of Mucopolysaccharidosis Type II
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 7, 2023 Category: Genetics & Stem Cells Authors: Shaun R. Wood Ahsan Chaudrhy Stuart Ellison Rachel Searle Constance Burgod Ghazala Tehseen Gabriella Forte Claire O'Leary H élène Gleitz Aiyin Liao James Cook Rebecca Holley Brian W. Bigger Source Type: research
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Authors: Carlos Munoz-Zuluaga Monica Gertz Melissa Yost-Bido Alessandria Greco Nicholas Gorman Alvin Chen Vikrum Kooner Jonathan B. Rosenberg Bishnu P. De Stephen M. Kaminsky Alain Borczuk Rodolfo J. Ricart Arbona Heather R. Martin Sebastien Monette Richie Khanna Source Type: research
Direct Knockdown of PDZ and LIM Domain 1 Using an Adenoviral Delivery System Accelerates Osteogenesis and Fracture Healing in Mice
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Authors: Zhiguang Chen Qi Zhao Ran Zhang Lianghong Chen Songlan Gao Yu Wang Tiegang Li Jinqi Xue Source Type: research
Characteristics, Recombination Methods, and Applications Progresses of Split-Cas9 System
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Authors: Zhixi Liu Lu Huang Han Deng Yan Chen Hongtao Xiao Source Type: research
Correction to: Inhibition of MicroRNA-9-5p Protects Against Cardiac Remodeling Following Myocardial Infarction in Mice, by Xiao et al. Hum Gene Ther 2019;30(3):286 –301; doi: 10.1089/hum.2018.059
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Source Type: research
Improvement of Precision in Recombinant Adeno-Associated Virus Infectious Titer Assay with Droplet Digital PCR as an Endpoint Measurement
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Authors: Tam Duong James McAllister Khalid Eldahan Jennifer Wang Eric Onishi Kate Shen Robert Schrock Bingnan Gu Peng Wang Source Type: research
MPZL1 Promotes Lung Adenocarcinoma Progression by Enhancing Tumor Proliferation, Invasion, Migration, and Suppressing Immune Function via Transforming Growth Factor- β1
Human Gene Therapy,Volume 34, Issue 11-12, Page 540-553, June 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - June 16, 2023 Category: Genetics & Stem Cells Authors: Ansheng Wang Fangtian Fan Chao Zang Chao Li Haining Hong Zuyi Wang Yuan Gao Liwei Chen Xiaofu Yu Chao Zhou Chengling Zhao Source Type: research
Food and Drug Administration Sets Stage for Approval of First Duchenne Muscular Dystrophy Gene Therapy
Human Gene Therapy,Volume 34, Issue 11-12, Page 477-480, June 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - June 16, 2023 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Long Non-Coding RNAs, Cell Cycle, and Human Breast Cancer
Human Gene Therapy,Volume 34, Issue 11-12, Page 481-494, June 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - June 16, 2023 Category: Genetics & Stem Cells Authors: Qinan Yin Haodi Ma Gayan Bamunuarachchi Xuewei Zheng Yan Ma Source Type: research
Complement Activation by Adeno-Associated Virus-Neutralizing Antibody Complexes
Human Gene Therapy,Volume 34, Issue 11-12, Page 554-566, June 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - June 15, 2023 Category: Genetics & Stem Cells Authors: Cara West Joel D. Federspiel Kara Rogers Arpana Khatri Sheila Rao-Dayton Mireia Fernandez Ocana Sean Lim Aaron Michael D'Antona Sandra Casinghino Suryanarayan Somanathan Source Type: research
Quantitation of Residual Host Cell DNA in Recombinant Adeno-Associated Virus Using Droplet Digital Polymerase Chain Reaction
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 22, 2023 Category: Genetics & Stem Cells Authors: Kiyoko Higashiyama Yuzhe Yuan Noriko Hashiba Kyoko Masumi-Koizumi Keisuke Yusa Kazuhisa Uchida Source Type: research
Advances in CRISPR/Cas9 Genome Editing for the Treatment of Muscular Dystrophies
Human Gene Therapy,Volume 34, Issue 9-10, Page 388-403, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Sina Fatehi Ryan M. Marks Matthew J. Rok Lucie Perillat Evgueni A. Ivakine Ronald D. Cohn Source Type: research
CRISPR-Editing Therapy for Duchenne Muscular Dystrophy
Human Gene Therapy,Volume 34, Issue 9-10, Page 379-387, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Francesco Chemello Eric N. Olson Rhonda Bassel-Duby Source Type: research
Immune Responses to Muscle-Directed Adeno-Associated Viral Gene Transfer in Clinical Studies
Human Gene Therapy,Volume 34, Issue 9-10, Page 365-371, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Sandeep R.P. Kumar Dongsheng Duan Roland W. Herzog Source Type: research
Progress in Bioengineering of Myotropic Adeno-Associated Viral Gene Therapy Vectors
Human Gene Therapy,Volume 34, Issue 9-10, Page 350-364, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Jixin Liu Teng Wei Koay Olena Maiakovska Margarita Zayas Dirk Grimm Source Type: research
