Brother of Cure Rare Disease CEO Dies in Trial of Duchenne Muscular Dystrophy Therapy
Human Gene Therapy,Volume 33, Issue 23-24, Page 1224-1227, December 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - December 14, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
ESGCT ; Abstract Author Index
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 25, 2022 Category: Genetics & Stem Cells Source Type: research
ESGCT 29th Annual Congress ; In collaboration with BSGCT ; Edinburgh, UK ; October 11 –14, 2022 ; Abstracts
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 25, 2022 Category: Genetics & Stem Cells Source Type: research
Suicide Gene Delivery System Mediated by Ultrasound-Targeted Microbubble Destruction: A Promising Strategy for Cancer Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 23, 2022 Category: Genetics & Stem Cells Authors: Tong Wu Chi Huang Yiran Yao Zhaolin Du Zhijun Liu Source Type: research
Phenotypic Correction of Murine Mucopolysaccharidosis Type II by Engraftment of Ex Vivo Lentiviral Vector-Transduced Hematopoietic Stem and Progenitor Cells
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 23, 2022 Category: Genetics & Stem Cells Authors: Miles C. Smith Lalitha R. Belur Andrea D. Karlen Olivia Erlanson Kelly M. Podetz-Pedersen Jessica McKenzie Jenn Detellis Khatuna Gagnidze Geoffrey Parsons Nicholas Robinson Shelby Labarre Saumil Shah Justin Furcich Troy C. Lund Hsing-Chen Tsai R. Scott Mc Source Type: research
Letter to the Editor: A Lesson for the Future —How Semantic Ambiguity Led to the Spread of Anti-Scientific Attitudes About COVID-19 mRNA Vaccines
Human Gene Therapy,Volume 33, Issue 21-22, Page 1213-1216, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Amir Asaleh Jichun Zhou Narges Rahmanian Source Type: research
Direct ITR-to-ITR Nanopore Sequencing of AAV Vector Genomes
Human Gene Therapy,Volume 33, Issue 21-22, Page 1187-1196, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Suk Namkung Ngoc Tam Tran Sangeetha Manokaran Ran He Qin Su Jun Xie Guangping Gao Phillip W.L. Tai Source Type: research
Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases
Human Gene Therapy,Volume 33, Issue 21-22, Page 1174-1186, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Jenny A. Greig Camilo Breton Scott N. Ashley Kelly M. Martins Cassandra Gorsuch Joanna K. Chorazeczewski Thomas Furmanak Melanie K. Smith Yanqing Zhu Peter Bell Wendy Shoop Hui Li Jeff Smith Ginger Tomberlin Peter Clark Thomas W. Mitchell Elizabeth L. Buz Source Type: research
Cellular and Structural Characterization of VP1 and VP2 Knockout Mutants of AAV3B Serotype and Implications for AAV Manufacturing
Human Gene Therapy,Volume 33, Issue 21-22, Page 1142-1156, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Iker Arriaga Aitor Navarro Amaia Etxabe C ésar Trigueros R. Jude Samulski Philippe Moullier Achille Fran çois Nicola G.A. Abrescia Source Type: research
Eli Lilly to Acquire Akouos for up to $610M
Human Gene Therapy,Volume 33, Issue 21-22, Page 1105-1108, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Call for Special Issue Papers: Genetic and Nongenetic Inflammation Networks in Major Human Diseases
Human Gene Therapy,Volume 33, Issue 21-22, Page 1103-1104, November 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Yan Ma Source Type: research
Engineering Cancer Selective Virotherapies: Are the Pieces of the Puzzle Falling into Place?
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 4, 2022 Category: Genetics & Stem Cells Authors: Emma A. Swift Steven M. Pollard Alan L. Parker Source Type: research
Identification of Broadly Applicable Adeno-Associated Virus Vectors by Systematic Comparison of Commonly Used Capsid Variants In Vitro
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 2, 2022 Category: Genetics & Stem Cells Authors: Jonas Weinmann Julia S öllner Sarah Abele Gudrun Zimmermann Kai Zuckschwerdt Christine Mayer Jenny Danner-Liskus Alexander Peltzer Michael Schuler Thorsten Lamla Benjamin Strobel Source Type: research
Immune Responses and Immunosuppressive Strategies for Adeno-Associated Virus-Based Gene Therapy for Treatment of Central Nervous System Disorders: Current Knowledge and Approaches
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 1, 2022 Category: Genetics & Stem Cells Authors: Suyash Prasad David P. Dimmock Benjamin Greenberg Jagdeep S. Walia Chanchal Sadhu Fatemeh Tavakkoli Gerald S. Lipshutz Source Type: research
Preclinical Evaluation of Foamy Virus Vector-Mediated Gene Addition in Human Hematopoietic Stem/Progenitor Cells for Correction of Leukocyte Adhesion Deficiency Type 1
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - November 1, 2022 Category: Genetics & Stem Cells Authors: Richard H. Smith Hanan Bloomer Danielle Fink Keyvan Keyvanfar Md Nasimuzzaman F átima Sancheznieto Roop Dutta Kacey Guenther Bui Luigi J. Alvarado Thomas R. Bauer Dennis D. Hickstein David W. Russell Punam Malik Johannes C.M. van der Loo Steven L. Highfi Source Type: research
