Efficacy and Safety of a Krabbe Disease Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 22, 2022 Category: Genetics & Stem Cells Authors: Juliette Hordeaux Brianne A. Jeffrey Jinlong Jian Gourav R. Choudhury Kristofer Michalson Thomas W. Mitchell Elizabeth L. Buza Jessica Chichester Cecilia Dyer Jessica Bagel Charles H. Vite Allison M. Bradbury James M. Wilson Source Type: research

Efficacy and Safety of FX201, a Novel Intra-Articular IL-1Ra Gene Therapy for Osteoarthritis Treatment, in a Rat Model
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 18, 2022 Category: Genetics & Stem Cells Authors: Rebecca Senter Rogely Boyce Marko Repic Emily Walsh Martin Monika Chabicovsky Genevi ève Langevin-Carpentier Agathe B édard Neil Bodick Source Type: research

Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Robert Klamroth Gregory Hayes Tatiana Andreeva Keith Gregg Takashi Suzuki Ismail Haroon Mitha Brandon Hardesty Midori Shima Toni Pollock Patricia Slev Johannes Oldenburg Margareth C. Ozelo Natalie Stieltjes Sabine-Marie Castet Johnny Mahlangu Flora Peyvan Source Type: research

CD19 or CD20 CAR T Cell Therapy Demonstrates Durable Antitumor Efficacy in Patients with Central Nervous System Lymphoma
Human Gene Therapy,Volume 33, Issue 5-6, Page 318-329, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Rui Liu Qian Cheng Liqing Kang Erhua Wang Ying Li Jian Zhang Han Xiao Yi Zhang Ling Chu Xin Chen Chang Zhang Jingwen Tan Nan Xu Minghao Li Lei Yu Xin Li Source Type: research

Role of Micro-RNA in the Regulation of Cell Polarization in Hepatocellular Carcinoma
Human Gene Therapy,Volume 33, Issue 5-6, Page 301-308, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Iman Nazar Talib Al-Ani Hadeer Akram Al-Ani Source Type: research

Nonhuman Primate Adenoviruses of the Human Adenovirus B Species Are Potent and Broadly Acting Oncolytic Vector Candidates
Human Gene Therapy,Volume 33, Issue 5-6, Page 275-289, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Selas T.F. Bots Vera Kemp Steve J. Cramer Diana J.M. van den Wollenberg Marten Hornsveld Martine L.M. Lamfers Gabri van der Pluijm Rob C. Hoeben Source Type: research

M11: A Tropism-Modified Oncolytic Adenovirus Arming with a Tumor-Homing Peptide for Advanced Ovarian Cancer Therapies
Human Gene Therapy,Volume 33, Issue 5-6, Page 262-274, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Fei Li Yuan Yuan Yun Dai Teng Cheng Heng Cao Danmei Yan Ying Li Qian Sun Xiaoyuan Huang Qinglei Gao Source Type: research

Evaluating Readministration of Adeno-Associated Virus for Gene Therapy
Human Gene Therapy,Volume 33, Issue 5-6, Page 218-220, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Motahareh Arjomandnejad Allison M. Keeler Source Type: research

Pfizer Eyes Resuming Phase III Enrollment, Investigates Phase Ib Death Tied to Duchenne Muscular Dystrophy Candidate
Human Gene Therapy,Volume 33, Issue 5-6, Page 215-217, March 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 16, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research

Reuben Matalon, MD, PhD, FACMG (1935 –2021)
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 3, 2022 Category: Genetics & Stem Cells Authors: Dena R. Matalon Gopalrao Velagaleti Seemin S. Ahmed Dominic J. Gessler Guangping Gao Source Type: research

Strategies for Optimization of the Clustered Regularly Interspaced Short Palindromic Repeat-Based Genome Editing System for Enhanced Editing Specificity
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 1, 2022 Category: Genetics & Stem Cells Authors: Yang-min Wang Hao-zheng Wang Ying-zhen Jian Zhong-tao Luo Hong-wei Shao Wen-feng Zhang Source Type: research

Correction to: Induced CD20 Expression on B-Cell Malignant Cells Heightened the Cytotoxic Activity of Chimeric Antigen Receptor Engineered T Cells, by Xu et al. Hum Gene Ther 2019;30(4):497 –510. DOI: 10.1089/hum.2018.119
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 1, 2022 Category: Genetics & Stem Cells Source Type: research

Therapeutic Efficacy of an Oncolytic Influenza Virus Carrying an Antibody Against Programmed Cell Death 1 in Hepatocellular Carcinoma
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 23, 2022 Category: Genetics & Stem Cells Authors: Guanglin Lei Baofa Li Hao Yang Fang Sun Donghui Li Jin Yan Yonggang Wang Ruisheng Li Honghong Liu Shaogeng Zhang Yufeng Li Penghui Yang Source Type: research

Letter to the Editor: Hematopoietic Stem and Progenitor Cell Mobilization and Collection for Patients Diagnosed with Osteopetrosis and Hurler Syndrome
Human Gene Therapy,Volume 33, Issue 3-4, Page 213-214, February 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Juli án Sevilla June Iriondo Elena Sebastian Marta Gonzalez-Vicent Jonathan D. Schwartz Josune Zubicaray Source Type: research

Biodistribution and Tolerability of AAV-PHP.B-CBh-SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles
Human Gene Therapy,Volume 33, Issue 3-4, Page 175-187, February 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Xavier Palazzi Ingrid D. Pardo Madhu P. Sirivelu Leah Newman Steven W. Kumpf Jessie Qian Tania Franks Sarah Lopes June Liu Laura Monarski Sandra Casinghino Casey Ritenour Hayley Ritenour Christopher Dubois Jennifer Olson John Graves Kristin E. Alexander T Source Type: research