Insight and Development of Advanced Recombinant Adeno-Associated Virus Analysis Tools Exploiting Single-Particle Quantification by Multidimensional Droplet Digital PCR
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 28, 2022 Category: Genetics & Stem Cells Authors: Jeanette Zanker Sara L ázaro-Petri Daniela H üser Regine Heilbronn Adrien Savy Source Type: research

Minimum Effective Dose to Achieve Biochemical Correction with Adeno-Associated Virus Vector-Mediated Gene Therapy in Mice with Pompe Disease
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 27, 2022 Category: Genetics & Stem Cells Authors: Sang-Oh Han Dorothy Gheorghiu Songtao Li Hye Ri Kang Dwight Koeberl Source Type: research

Prevalence of Pre-Existing Neutralizing Antibodies Against Adeno-Associated Virus Serotypes 1, 2, 5, 6, 8, and 9 in Sera of Different Pig Strains
Human Gene Therapy,Volume 33, Issue 7-8, Page 451-459, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Yanshan Dai Uma Kavita Margit H. Lampen Sander Gielen Glen Banks Paul Levesque Alexander Kozhich Renuka Pillutla Yan Zhang Vibha Jawa Leonard Adam Source Type: research

In Vivo Hematopoietic Stem Cell Gene Therapy for SARS-CoV2 Infection Using a Decoy Receptor
Human Gene Therapy,Volume 33, Issue 7-8, Page 389-403, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Hongjie Wang Chang Li Adebimpe O. Obadan Hannah Frizzell Tien-Ying Hsiang Sucheol Gil Audrey Germond Connie Fountain Audrey Baldessari Steve Roffler Hans-Peter Kiem Deborah H. Fuller Andr é Lieber Source Type: research

Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity
Human Gene Therapy,Volume 33, Issue 7-8, Page 371-388, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Ngoc Tam Tran Emilie Lecomte Sylvie Saleun Suk Namkung C écile Robin Kristina Weber Eric Devine Veronique Blouin Oumeya Adjali Eduard Ayuso Guangping Gao Magalie Penaud-Budloo Phillip W.L. Tai Source Type: research

Recombinant Adeno-Associated Virus Production, the Beginning of the End of Uncertainty
Human Gene Therapy,Volume 33, Issue 7-8, Page 355-357, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Weidong Xiao R. Jude Samulski Source Type: research

Bluebird Bio Chief Financial Officer Resigns as Company Raises “Going Concern” Doubts
Human Gene Therapy,Volume 33, Issue 7-8, Page 351-354, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research

Interview with Beverly Davidson, PhD
Human Gene Therapy,Volume 33, Issue 7-8, Page 347-350, April 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 19, 2022 Category: Genetics & Stem Cells Authors: Thomas Gallagher Source Type: research

A Modified Arrestin1 Increases Lactate Production in the Retina and Slows Retinal Degeneration
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 18, 2022 Category: Genetics & Stem Cells Authors: Tiffany S. Nelson Chiab Simpson Frank Dyka Astra Dinculescu W. Clay Smith Source Type: research

Overexpression of G Protein-Coupled Receptor 40 Protects Obesity-Induced Cardiomyopathy Through the SIRT1/LKB1/AMPK Pathway
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 18, 2022 Category: Genetics & Stem Cells Authors: Sheng-Nan Li Ya-Lin Yu Bo-Yang Wang Shi-Yuan Qiao Mao-Mao Hu Han Wang Chang-Ning Fu Bo Dong Source Type: research

An Optimized CRISPR/Cas9 Adenovirus Vector (AdZ-CRISPR) for High-Throughput Cloning of sgRNA, Using Enhanced sgRNA and Cas9 Variants
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 18, 2022 Category: Genetics & Stem Cells Authors: Evelina Statkute Eddie C.Y. Wang Richard J. Stanton Source Type: research

International Conference on Lymphocyte Engineering Author Index
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 30, 2022 Category: Genetics & Stem Cells Source Type: research

International Conference on Lymphocyte Engineering ; 31 March –2 April 2022 ; Munich, Germany
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 30, 2022 Category: Genetics & Stem Cells Source Type: research

Retraction of: HOXD-AS1 Exerts Oncogenic Functions and Promotes Chemoresistance in Cisplatin-Resistant Cervical Cancer Cells by Chi et al. (doi: 10.1089/hum.2017.256)
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 28, 2022 Category: Genetics & Stem Cells Source Type: research

Efficacy and Safety of a Krabbe Disease Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 22, 2022 Category: Genetics & Stem Cells Authors: Juliette Hordeaux Brianne A. Jeffrey Jinlong Jian Gourav R. Choudhury Kristofer Michalson Thomas W. Mitchell Elizabeth L. Buza Jessica Chichester Cecilia Dyer Jessica Bagel Charles H. Vite Allison M. Bradbury James M. Wilson Source Type: research