Genetic Modification of the AAV5 Capsid with Lysine Residues Results in a Lung-Tropic Liver-Detargeted Gene Transfer Vector
Human Gene Therapy,Volume 33, Issue 3-4, Page 148-154, February 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Katie M. Stiles Esther Z. Frenk Stephen M. Kaminsky Ronald G. Crystal Source Type: research
Rational Use of Immunosuppressive Corticosteroids in Liver-Directed Adeno-Associated Virus Gene Therapy Studies
Human Gene Therapy,Volume 33, Issue 3-4, Page 116-118, February 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Ishani Dasgupta Allison M. Keeler Source Type: research
After Patient Death, FDA Places Hold on Pfizer Duchenne Muscular Dystrophy Gene Therapy Trial
Human Gene Therapy,Volume 33, Issue 3-4, Page 111-115, February 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Higher Seroprevalence of Anti-Adeno-Associated Viral Vector Neutralizing Antibodies Among Racial Minorities in the United States
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - February 2, 2022 Category: Genetics & Stem Cells Authors: Arpana Khatri Rajani Shelke Shunjie Guan Suryanarayan Somanathan Source Type: research
Acknowledgment of Reviewers 2021
Human Gene Therapy,Volume 33, Issue 1-2, Page 109-110, January 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Source Type: research
Allele-Specific Knockdown of Mutant Huntingtin Protein via Editing at Coding Region Single Nucleotide Polymorphism Heterozygosities
Human Gene Therapy,Volume 33, Issue 1-2, Page 25-36, January 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Authors: Sarah R. Oikemus Edith L. Pfister Ellen Sapp Kathryn O. Chase Lori A. Kennington Edward Hudgens Rachael Miller Lihua Julie Zhu Akanksh Chaudhary Eric O. Mick Miguel Sena-Esteves Scot A. Wolfe Marian DiFiglia Neil Aronin Michael H. Brodsky Source Type: research
Gene Therapy for Huntington's Disease: The Future Is in Gene Editing
Human Gene Therapy,Volume 33, Issue 1-2, Page 12-13, January 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Authors: Ana Rita Batista Source Type: research
Astellas, Dyno to Develop Next-Generation Adeno-Associated Virus Vectors in Up-to-$1.6B Partnership
Human Gene Therapy,Volume 33, Issue 1-2, Page 8-11, January 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Adeno-Associated Virus Delivery Limitations for Neurological Indications
Human Gene Therapy,Volume 33, Issue 1-2, Page 1-7, January 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 17, 2022 Category: Genetics & Stem Cells Authors: Hector Ribeiro Benatti Heather L. Gray-Edwards Source Type: research
Efficient and Precise Processing of the Optimized Primary Artificial MicroRNA in a Huntingtin-Lowering Adeno-Associated Viral Gene Therapy In Vitro and in Mice and Nonhuman Primates
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 10, 2022 Category: Genetics & Stem Cells Authors: Wei Wang Pengcheng Zhou Xin Wang Fen Chen Emily Christensen Jeffrey Thompson Xiaoqin Ren Adrian Kells Lisa Stanek Todd Carter Jay Hou Dinah W.Y. Sah Source Type: research
Short-Term Steroid Treatment of Rhesus Macaque Increases Transduction
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 7, 2022 Category: Genetics & Stem Cells Authors: Murali K. Yanda Vartika Tomar Cristina Valeria Cebotaru William B. Guggino Liudmila Cebotaru Source Type: research
Intra-Articular Adeno-Associated Virus-Mediated Proteoglycan 4 Gene Therapy for Preventing Posttraumatic Osteoarthritis
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 7, 2022 Category: Genetics & Stem Cells Authors: Dongrim Seol Hyeong Hun Choe Hongjun Zheng Marc J. Brouillette Douglas C. Fredericks Emily B. Petersen Ino Song Leela R.J. Chakka Aliasger K. Salem James A. Martin Source Type: research
Modulation of Immune Reaction in Hydrodynamic Gene Therapy for Hemophilia A
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 7, 2022 Category: Genetics & Stem Cells Authors: Mei Zhao Yi-Dan Sun Mengdi Yin Juan-Juan Zhao Si-Ang Li Guohua Li Feng Zhang Jing Xu Fei-Ying Meng Beldon Zhang Xin-Yu Sun Jian-Ping Zhang Tao Cheng Xiao-Bing Zhang Source Type: research
Preferential Expansion of Human CD34+CD133+CD90+ Hematopoietic Stem Cells Enhances Gene-Modified Cell Frequency for Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 7, 2022 Category: Genetics & Stem Cells Authors: Abisha Crystal Christopher Vigneshwaran Venkatesan Karthik V. Karuppusamy Saranya Srinivasan Prathibha Babu Manoj Kumar K. Azhagiri Karthik Chambayil Abhirup Bagchi Vignesh Rajendiran Nithin Sam Ravi Sanjay Kumar Srujan Kumar Marepally Kumarasamypet Murug Source Type: research
Genetic Modification of Limbs Using Ex Vivo Machine Perfusion
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - January 6, 2022 Category: Genetics & Stem Cells Authors: Emilio Valdivia Tamina Rother Yuliia Yuzefovych Franziska Hack Nadine Wenzel Rainer Blasczyk Nicco Krezdorn Constanca Figueiredo Source Type: research
