Duchenne Muscular Dystrophy Gene Therapy in 2023: Status, Perspective, and Beyond
Human Gene Therapy,Volume 34, Issue 9-10, Page 345-349, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Dongsheng Duan Source Type: research
CRISPR Therapeutics, Vertex Complete Rolling Biologics License Applications for Exa-Cel in Sickle Cell Disease, Beta Thalassemia
Human Gene Therapy,Volume 34, Issue 9-10, Page 341-344, May 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
AAV6-Mediated Gene Therapy Prevents Developmental Dentin Defects in a Dentinogenesis Imperfecta Type Ⅲ Mouse Model
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 17, 2023 Category: Genetics & Stem Cells Authors: Jing Fu Huiwen Zheng Yangyun Ou Guobin Yang Zhi Chen Guohua Yuan Source Type: research
Gene Supplementation in Mice Heterozygous for the D477G RPE65 Variant Implicated in Autosomal Dominant Retinitis Pigmentosa
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2023 Category: Genetics & Stem Cells Authors: Kecia L. Feathers Lin Jia Naheed W. Khan Alexander J. Smith Jian-Xing Ma Robin R. Ali Debra A. Thompson Source Type: research
Characterization of the Roles of Suppressor of Cytokine Signaling-3 in Esophageal Carcinoma
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 10, 2023 Category: Genetics & Stem Cells Authors: Xiaojie Yang Mengyue Tian Yukang Lin Liming Li Xinhai Sun Zhenyang Zhang Mingqiang Kang Jiangbo Lin Source Type: research
Correction to: Letter to the Editor: A Favorable Benefit –Risk Balance Maybe Expected with Replication-Defective Adenovirus-Mediated Interferon Gene Therapy for Cancer Treatment, by Qin Hum Gene Ther 2023;34(7-8):339–340; doi: 10.1089/hum.2023.028
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 8, 2023 Category: Genetics & Stem Cells Source Type: research
Correction to: Assessment of Pre-Clinical Liver Models Based on Their Ability to Predict the Liver-Tropism of Adeno-Associated Virus Vectors, by Westhaus et al. Hum Gene Ther 2023;34(7-8):273 –288; doi: 10.1089/hum.2022.188
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 8, 2023 Category: Genetics & Stem Cells Source Type: research
Optogenetic Control of Muscles: Potential Uses and Limitations
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 5, 2023 Category: Genetics & Stem Cells Authors: E. Myfanwy Cohen Fiona L. Knapman Lynne E. Bilston Source Type: research
The Future of Exon Skipping for Duchenne Muscular Dystrophy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 3, 2023 Category: Genetics & Stem Cells Authors: Annemieke Aartsma-Rus Source Type: research
Correction to: Genome Editing of Pik3cd Impedes Abnormal Retinal Angiogenesis, by Wu et al. Hum Gene Ther 2023;34(1-2):30-41; doi: 10.1089/hum.2022.079
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 3, 2023 Category: Genetics & Stem Cells Source Type: research
Lifelong Outcomes of Systemic Adeno-Associated Virus Micro-Dystrophin Gene Therapy in a Murine Duchenne Muscular Dystrophy Model
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 2, 2023 Category: Genetics & Stem Cells Authors: Nalinda B. Wasala Yongping Yue Bryan Hu Jin-Hong Shin Gang Yao Dongsheng Duan Source Type: research
Secretion of 4-1BB Ligand Crosslinked to PD-1 Checkpoint Inhibitor Potentiates Chimeric Antigen Receptor T Cell Solid Tumor Efficacy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 20, 2023 Category: Genetics & Stem Cells Authors: Zachary S. Dunn Yun Qu Melanie MacMullan Xianhui Chen Gunce Cinay Pin Wang Source Type: research
A Review of the Legislation of Direct-to-Consumer Genetic Testing in China
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 18, 2023 Category: Genetics & Stem Cells Authors: Chen Yichao Li Wei Chen Jiajv Source Type: research
Letter to the Editor: A Favorable Benefit –Risk Balance Maybe Expected with Replication-Defective Adenovirus-Mediated Interferon Gene Therapy for Cancer Treatment
Human Gene Therapy,Volume 34, Issue 7-8, Page 339-340, April 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 17, 2023 Category: Genetics & Stem Cells Authors: Albert Qin Source Type: research
Application of Size Exclusion Chromatography with Multiangle Light Scattering in the Analytical Development of a Preclinical Stage Gene Therapy Program
Human Gene Therapy,Volume 34, Issue 7-8, Page 325-338, April 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 17, 2023 Category: Genetics & Stem Cells Authors: Bryan Troxell I-Wei Tsai Kinjal Shah Christopher I. Knuckles Sarah Shelton Kate Lindsey Selene M. Barbosa Cardenas Taylor Roberts Source Type: research
