How Great a Risk Do You Take? A Qualitative Study Exploring Attitudes of Individuals with Friedreich Ataxia Toward Gene Therapy
Human Gene Therapy,Volume 34, Issue 19-20, Page 1041-1048, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Katherine Lieschke Varlli Scott Martin B. Delatycki Sharon Lewis Megan Munsie Claire Tanner Louise A. Corben Source Type: research

Clinical Efficacy and Safety of AdV-tk Gene Therapy for Patients with Cervical Squamous Intraepithelial Lesion: A Prospective Study
Human Gene Therapy,Volume 34, Issue 19-20, Page 1033-1040, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Nan Wang Xiulan Li Xin Liu Meina Bian Ying Hou Yuxiang Zhou Yanmei Li Fuqiang Xu Huadong Tang Ning Li Qing Liu Source Type: research

Significant Differences in Capsid Properties and Potency Between Adeno-Associated Virus Vectors Produced in Sf9 and HEK293 Cells
Human Gene Therapy,Volume 34, Issue 19-20, Page 1003-1021, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: April Giles Martin Lock Shu-Jen Chen Kevin Turner Gregg Wesolowski Andrew Prongay Boris N. Petkov Kanyin Olagbegi Hanying Yan James M. Wilson Source Type: research

Gene Therapy for Immunoglobulin E, Complement-Mediated, and Eosinophilic Disorders
Human Gene Therapy,Volume 34, Issue 19-20, Page 986-1002, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Odelya E. Pagovich Ronald G. Crystal Source Type: research

Up to $1.5B in Milestones as Otsuka, Shape Partner on Eye Disease Gene Therapies
Human Gene Therapy,Volume 34, Issue 19-20, Page 983-985, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research

Letter from Terry's Parents
Human Gene Therapy,Volume 34, Issue 19-20, Page 982-982, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Linda   Terry Horgan Source Type: research

Cure Rare Disease: An Initiative to Enable N of 1 Gene Editing
Human Gene Therapy,Volume 34, Issue 19-20, Page 980-981, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Richard W. Horgan Source Type: research

What We Owe Terry Horgan: Reflections from Providers, Family, and Scientists
Human Gene Therapy,Volume 34, Issue 19-20, Page 976-979, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Source Type: research

Special Editorial Feature: Learning from Our Failures
Human Gene Therapy,Volume 34, Issue 19-20, Page 975-975, October 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 16, 2023 Category: Genetics & Stem Cells Authors: Terence R. Flotte Source Type: research

Kallistatin Improves High-Fat-Induced Insulin Resistance via Epididymal Adipose Tissue-Derived Exosomes
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - October 4, 2023 Category: Genetics & Stem Cells Authors: Zi-Wei Yang Jing-Jing Ji Yu Jiang Ya Wu Jia-Qi Guo Gen-Shan Ma Yu-Yu Yao Source Type: research

Establishment of the Effectiveness of Early Versus Late Stem Cell Gene Therapy in Mucopolysaccharidosis II for Treating Central Versus Peripheral Disease
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - August 30, 2023 Category: Genetics & Stem Cells Authors: Oriana Mandolfo Aiyin Liao Esha Singh Claire O'leary Rebecca J. Holley Brian W. Bigger Source Type: research

International Conference on Lymphocyte Engineering Author Index
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - August 23, 2023 Category: Genetics & Stem Cells Source Type: research

International Conference on Lymphocyte Engineering ; 12 –14 September 2023 ; Munich, Germany
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - August 23, 2023 Category: Genetics & Stem Cells Source Type: research

Artificial Downregulation of Ribosomal Protein L34 Restricts the Proliferation and Metastasis of Colorectal Cancer by Suppressing the JAK2/STAT3 Signaling Pathway
Human Gene Therapy,Volume 34, Issue 15-16, Page 719-731, August 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - August 16, 2023 Category: Genetics & Stem Cells Authors: Yi-Chao Liang Rui Li Shu-Rui Bao Zhi-Long Li Hong-Zhuan Yin Chao-Liu Dai Source Type: research

An Engineered Adeno-Associated Virus Capsid Mediates Efficient Transduction of Pericytes and Smooth Muscle Cells of the Brain Vasculature
Human Gene Therapy,Volume 34, Issue 15-16, Page 682-696, August 2023. (Source: Human Gene Therapy)
Source: Human Gene Therapy - August 16, 2023 Category: Genetics & Stem Cells Authors: Servio H. Ramirez Jonathan F. Hale Siobhan McCarthy Christian L. Cardenas Kalpani N. Udeni Galpayage Dona Killian S. Hanlon Eloise Hudry Demitri De La Cruz Carrie Ng Sabyasachi Das Diane M. Nguyen Josette Nammour Rachel E. Bennett Allison M. Andrews Patri Source Type: research