Biodistribution and Tolerability of AAV-PHP.B-CBh-SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles

Human Gene Therapy,Volume 33, Issue 3-4, Page 175-187, February 2022.

Source: Human Gene Therapy - February 14, 2022 Category: Genetics & Stem Cells Authors: Xavier Palazzi Ingrid D. Pardo Madhu P. Sirivelu Leah Newman Steven W. Kumpf Jessie Qian Tania Franks Sarah Lopes June Liu Laura Monarski Sandra Casinghino Casey Ritenour Hayley Ritenour Christopher Dubois Jennifer Olson John Graves Kristin E. Alexander T Source Type: research