After He Jiankui's Case: Chinese Legislative Modifications in Human Embryo Gene Editing
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 20, 2022 Category: Genetics & Stem Cells Authors: Yichao Chen Shuren Tao Jiajv Chen Wei Li Source Type: research
Efficient Delivery of Adeno-Associated Virus into Inner Ear In Vivo Through Trans-Stapes Route in Adult Guinea Pig
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 19, 2022 Category: Genetics & Stem Cells Authors: Jinghan Wang Liping Zhao Xi Gu Yuanyuan Xue Shengyi Wang Ru Xiao Luk H. Vandenberghe Kevin A. Peng Yilai Shu Huawei Li Source Type: research
Gene Therapy in Opn1mw −/−/Opn1sw−/− Mice and Implications for Blue Cone Monochromacy Patients with Deletion Mutations
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2022 Category: Genetics & Stem Cells Authors: Xiajie Ma Emily R. Sechrest Diego Fajardo Ping Zhu Frank Dyka Yixiao Wang Ekaterina Lobanova Shannon E. Boye Wolfgang Baehr Wen-Tao Deng Source Type: research
Conversion of the Liver into a Biofactory for DNaseI Using Adeno-Associated Virus Vector Gene Transfer Reduces Neutrophil Extracellular Traps in a Model of Systemic Lupus Erythematosus
Human Gene Therapy,Volume 33, Issue 9-10, Page 560-571, May 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2022 Category: Genetics & Stem Cells Authors: Amina Ahmad Mawj Mandwie Kim M. O'Sullivan Christine Smyth Jarrod York Helen Doyle Stephen R. Holdsworth Matthew C. Pickering Peter J. Lachmann Ian E. Alexander Grant J. Logan Source Type: research
Endobronchial Aerosolized AAV1.SERCA2a Gene Therapy in a Pulmonary Hypertension Pig Model: Addressing the Lung Delivery Bottleneck
Human Gene Therapy,Volume 33, Issue 9-10, Page 550-559, May 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2022 Category: Genetics & Stem Cells Authors: Olympia Bikou Serena Tharakan Kelly P. Yamada Taro Kariya Jaume Aguero Alexandra Gordon Renata Mazurek Tadao Aikawa Erik Kohlbrenner Kenneth M. Fish Roger J. Hajjar Kiyotake Ishikawa Source Type: research
Gene Therapy and the Use of Animal Models: Why Mice Alone Are Not Sufficient
Human Gene Therapy,Volume 33, Issue 9-10, Page 477-478, May 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2022 Category: Genetics & Stem Cells Authors: Alisha M. Gruntman Terence R. Flotte Source Type: research
Bluebird Bio Eliminating 30% of Staff in Restructuring
Human Gene Therapy,Volume 33, Issue 9-10, Page 473-476, May 2022. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 16, 2022 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Suppressing Nonsense for Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 10, 2022 Category: Genetics & Stem Cells Authors: Barrie J. Carter Source Type: research
Development of a Beta Cell-Specific Expression Control Element for Recombinant Adeno-Associated Virus
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 10, 2022 Category: Genetics & Stem Cells Authors: Sunghee Chai Youngjin Kim Feorillo Galivo Craig Dorrell Leslie Wakefield Jeffrey Posey Amanda M. Ackermann Klaus H. Kaestner Matthias Hebrok Markus Grompe Source Type: research
Single-Dose Intrathecal Dorsal Root Ganglia Toxicity of Onasemnogene Abeparvovec in Cynomolgus Monkeys
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 9, 2022 Category: Genetics & Stem Cells Authors: Francis Fonyuy Tukov Keith Mansfield Mark Milton Emily Meseck Kelley Penraat Deepa Chand Andreas Hartmann Source Type: research
AAV-p40 Bioengineering Platform for Variant Selection Based on Transgene Expression
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 6, 2022 Category: Genetics & Stem Cells Authors: Adrian Westhaus Marti Cabanes-Creus Timo Jonker Erwan Sallard Renina Gale Navarro Erhua Zhu Grober Baltazar Torres Scott Lee Patrick Wilmott Anai Gonzalez-Cordero Giorgia Santilli Adrian J. Thrasher Ian E. Alexander Leszek Lisowski Source Type: research
The Effect of Rapamycin and Ibrutinib on Antibody Responses to Adeno-Associated Virus Vector-Mediated Gene Transfer
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 4, 2022 Category: Genetics & Stem Cells Authors: Zhiquan Xiang Klaudia Kuranda William Quinn Areski Chekaoui Robert Ambrose Mohadeseh Hasanpourghai Mikhail Novikov Dakota Newman Christina Cole Xiangyang Zhou Federico Mingozzi Hildegund C.J. Ertl Source Type: research
Efficacious Androgen Hormone Administration in Combination with Adeno-Associated Virus Vector-Mediated Gene Therapy in Female Mice with Pompe Disease
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 4, 2022 Category: Genetics & Stem Cells Authors: Sang-oh Han Dorothy Gheorghiu Alex Chang Sweet Hope Mapatano Songtao Li Elizabeth Brooks Dwight Koeberl Source Type: research
Bone Marrow Mesenchymal Stem Cell-Mediated Radiosensitive Promoter-Combined Sodium Iodide Symporter for the Treatment of Breast Cancer
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 4, 2022 Category: Genetics & Stem Cells Authors: Lu Zhang Yue Xi Rui Guo Ying Miao Hong Chen Min Zhang Biao Li Source Type: research
The gRNA Vector Level Determines the Outcome of Systemic AAV CRISPR Therapy for Duchenne Muscular Dystrophy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - May 4, 2022 Category: Genetics & Stem Cells Authors: Nalinda B. Wasala Emily D. Million Thais B. Watkins Lakmini P. Wasala Jin Han Yongping Yue Baisong Lu Shi-jie Chen Chady H. Hakim Dongsheng Duan Source Type: research
