The gRNA Vector Level Determines the Outcome of Systemic AAV CRISPR Therapy for Duchenne Muscular Dystrophy

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - May 4, 2022 Category: Genetics & Stem Cells Authors: Nalinda B. Wasala Emily D. Million Thais B. Watkins Lakmini P. Wasala Jin Han Yongping Yue Baisong Lu Shi-jie Chen Chady H. Hakim Dongsheng Duan Source Type: research