Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases

Human Gene Therapy,Volume 33, Issue 21-22, Page 1174-1186, November 2022.

Source: Human Gene Therapy - November 14, 2022 Category: Genetics & Stem Cells Authors: Jenny A. Greig Camilo Breton Scott N. Ashley Kelly M. Martins Cassandra Gorsuch Joanna K. Chorazeczewski Thomas Furmanak Melanie K. Smith Yanqing Zhu Peter Bell Wendy Shoop Hui Li Jeff Smith Ginger Tomberlin Peter Clark Thomas W. Mitchell Elizabeth L. Buz Source Type: research