Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia

Human Gene Therapy, Ahead of Print.

Source: Human Gene Therapy - July 4, 2023 Category: Genetics & Stem Cells Authors: Carlos Munoz-Zuluaga Monica Gertz Melissa Yost-Bido Alessandria Greco Nicholas Gorman Alvin Chen Vikrum Kooner Jonathan B. Rosenberg Bishnu P. De Stephen M. Kaminsky Alain Borczuk Rodolfo J. Ricart Arbona Heather R. Martin Sebastien Monette Richie Khanna Source Type: research