Prodromal Parkinsonian Features in GBA1 Mutation Carriers
Conditions:   Gaucher Disease, Type 1;   Healthy Intervention:   Diagnostic Test: The investigators aim to identify prodromal PD in a cohort of carriers of Gaucher disease. Sponsor:   Shaare Zedek Medical Center Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 24, 2022 Category: Research Source Type: clinical trials

Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3
Condition:   Gaucher's Disease Type III Interventions:   Drug: Venglustat;   Drug: imiglucerase Sponsor:   Genzyme, a Sanofi Company Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 3, 2022 Category: Research Source Type: clinical trials