Prodromal Parkinsonian Features in GBA1 Mutation Carriers
Conditions: Gaucher Disease, Type 1; Healthy Intervention: Diagnostic Test: The investigators aim to identify prodromal PD in a cohort of carriers of Gaucher disease. Sponsor: Shaare Zedek Medical Center Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 24, 2022 Category: Research Source Type: clinical trials
Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3
Condition: Gaucher's Disease Type III Interventions: Drug: Venglustat; Drug: imiglucerase Sponsor: Genzyme, a Sanofi Company Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 3, 2022 Category: Research Source Type: clinical trials