Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)
Condition: Gaucher Disease, Type 2 Intervention: Biological: PR001 Sponsor: Prevail Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 2, 2020 Category: Research Source Type: clinical trials
Phase 1/2 Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition: Gaucher Disease Intervention: Drug: AVR-RD-02 Sponsor: AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials
Phase 1/2 Safety & Efficacy Study, Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition: Gaucher Disease Intervention: Drug: AVR-RD-02 Sponsor: AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials
Phase 1/2 Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition: Gaucher Disease Intervention: Drug: AVR-RD-02 Sponsor: AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials