Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)
Condition:   Gaucher Disease, Type 2 Intervention:   Biological: PR001 Sponsor:   Prevail Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 2, 2020 Category: Research Source Type: clinical trials

Phase 1/2 Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition:   Gaucher Disease Intervention:   Drug: AVR-RD-02 Sponsor:   AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials

Phase 1/2 Safety & Efficacy Study, Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition:   Gaucher Disease Intervention:   Drug: AVR-RD-02 Sponsor:   AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials

Phase 1/2 Lentiviral Vector Gene Therapy AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Condition:   Gaucher Disease Intervention:   Drug: AVR-RD-02 Sponsor:   AvroBio Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 30, 2019 Category: Research Source Type: clinical trials