Magnetic resonance spectroscopy biomarkers in type 3 gaucher disease (gd3)
Condition: Gaucher Disease, Type 3 Intervention: Other: No intervention Sponsor: University of Minnesota Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - October 19, 2022 Category: Research Source Type: clinical trials
A Study of Velaglucerase Alfa (VPRIV) in Chinese Children, Teenagers, and Adults With Type 1 Gaucher Disease
Condition: Gaucher Disease Intervention: Drug: Velaglucerase Alfa Sponsor: Takeda Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 7, 2022 Category: Research Source Type: clinical trials