A Second-generation AI Based Therapeutic Regimen in Patients With Gaucher Disease Treated With Enzyme Replacement Therapy.
Conditions: Gaucher Disease Type 1 Interventions: Combination Product: Enzyme replacement therapy for Gaucher disease in combination with altus care application Sponsors: Hadassah Medical Organization Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 22, 2023 Category: Research Source Type: clinical trials
GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma
Conditions: Gaucher Disease; Acid SphingoMyelinase Deficiency Intervention: Sponsor: Fundación Española de Hematología y Hemoterapía Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 15, 2023 Category: Research Source Type: clinical trials
Implementation and Evaluation of a Rare Disease Algorithm to Identify Persons at Risk of Gaucher Disease Using Data From Electronic Health Records (EHRs) in the United States (Project Searchlight)
Condition: Gaucher Disease Intervention: Procedure: Investigational procedure Sponsor: Sanofi Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 19, 2023 Category: Research Source Type: clinical trials