Phase 1/2 Study of CAN103 in Newly Treated Subjects With Gaucher Disease
Conditions: Gaucher Disease, Type 1; Gaucher Disease, Type 3 Interventions: Drug: Low-dose CAN103; Drug: High-dose CAN103 Sponsor: CANbridge (Suzhou) Bio-pharma Co., Ltd. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 7, 2022 Category: Research Source Type: clinical trials
Phase 1/2 Study of CAN103 in Subjects With Gaucher Disease
Conditions: Gaucher Disease, Type 1; Gaucher Disease, Type 3 Interventions: Drug: Low-dose CAN103; Drug: High-dose CAN103 Sponsor: CANbridge (Suzhou) Bio-pharma Co., Ltd. Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 7, 2022 Category: Research Source Type: clinical trials
A Gene Therapy Study in Patients With Gaucher Disease Type 1
Condition: Gaucher Disease, Type 1 Intervention: Genetic: FLT201 Sponsor: Freeline Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 13, 2022 Category: Research Source Type: clinical trials