A Multicenter, Safety and Efficacy Study of Taliglucerase Alfa in Subjects With Type 3 Gaucher Disease
Condition: Gaucher Disease, Type 3 Intervention: Drug: Elelyso Sponsors: Ari Zimran; Pfizer Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 1, 2019 Category: Research Source Type: clinical trials
Ambroxol Therapy for Patients With Type 1 Gaucher Disease and Suboptimal Response to Enzyme Replacement Therapy
Condition: Gaucher Disease, Type 1 Intervention: Drug: Ambroxol Sponsor: Shaare Zedek Medical Center Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 15, 2019 Category: Research Source Type: clinical trials