A Multicenter, Safety and Efficacy Study of Taliglucerase Alfa in Subjects With Type 3 Gaucher Disease
Condition:   Gaucher Disease, Type 3 Intervention:   Drug: Elelyso Sponsors:   Ari Zimran;   Pfizer Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - July 1, 2019 Category: Research Source Type: clinical trials

Ambroxol Therapy for Patients With Type 1 Gaucher Disease and Suboptimal Response to Enzyme Replacement Therapy
Condition:   Gaucher Disease, Type 1 Intervention:   Drug: Ambroxol Sponsor:   Shaare Zedek Medical Center Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 15, 2019 Category: Research Source Type: clinical trials