An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher Disease
Conditions: Type II Gaucher Disease Interventions: Drug: VGN-R08b Sponsors: Xinhua Hospital, Shanghai Jiao Tong University School of Medicine; Shanghai Vitalgen BioPharma Co., Ltd. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 22, 2024 Category: Research Source Type: clinical trials
Screening for Gaucher Disease and Acid Sphingomyelinase Deficiency
Conditions: Gaucher Disease Sponsors: Chung-Hsing Wang; Sanofi Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 14, 2024 Category: Research Source Type: clinical trials
Role of Vitamin E in Gaucher Disease Patients
Conditions: Gaucher Disease Interventions: Drug: Vitamin E Sponsors: Ain Shams University Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 18, 2024 Category: Research Source Type: clinical trials
A Study to Evaluate Pharmacokinetic Parameters and Safety of Eliglustat Absorption Through the Mouth
Conditions: Gaucher ' s Disease Interventions: Drug: Eliglustat Sponsors: Sanofi Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 5, 2024 Category: Research Source Type: clinical trials
A Study to Evaluate Pharmacokinetic Parameters of Eliglustat in Healthy Volunteers Who Are CYP2D6 Extensive or Poor Metabolizers
Conditions: Gaucher ' s Disease Interventions: Drug: Eliglustat Sponsors: Sanofi Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 3, 2024 Category: Research Source Type: clinical trials
A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type I
Conditions: Gaucher Disease Type I Interventions: Biological: LY-M001 Injection Sponsors: He Huang; Lingyi Biotech Co., Ltd. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - December 8, 2023 Category: Research Source Type: clinical trials
A Study to Evaluate Absolute Bioavailability, Absorption, Metabolism, and Excretion of Genz-112638 in Healthy Male Participants
Conditions: Gaucher ' s Disease Type I Interventions: Drug: Genz-112638; Drug: Genz-112638; Drug: [14C]-Genz-112638 Sponsors: Sanofi Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 22, 2023 Category: Research Source Type: clinical trials
Biomarkers Related to Bone in Pediatric Gaucher Disease Related to Bone Pathology in Pediatric Patients With Gaucher Disease
Conditions: Gaucher Disease; Bone Diseases Sponsors: Lysosomal and Rare Disorders Research and Treatment Center, Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 3, 2023 Category: Research Source Type: clinical trials
Plasma Biomarkers Related to Bone in Pediatric Gaucher Disease Related to Bone Pathology in Pediatric Patients With Gaucher Disease
Conditions: Gaucher Disease; Bone Diseases Sponsors: Lysosomal and Rare Disorders Research and Treatment Center, Inc. Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 3, 2023 Category: Research Source Type: clinical trials
A Second-generation AI Based Therapeutic Regimen in Patients With Gaucher Disease Treated With Enzyme Replacement Therapy.
Condition: Gaucher Disease Type 1 Intervention: Combination Product: Enzyme replacement therapy for Gaucher disease in combination with altus care application Sponsor: Hadassah Medical Organization Completed (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 22, 2023 Category: Research Source Type: clinical trials
