Potential Disease-Modifying Effects of Lithium Carbonate in Niemann-Pick Disease, Type C1

Conclusion: Lithium is a potential therapeutic option for NP-C1 patients. Larger randomized and double-blind clinical trials are needed to further support this finding.Clinical Trial Registration:ClinicalTrials.gov, NCT03201627.
Source: Frontiers in Pharmacology - Category: Drugs & Pharmacology Source Type: research