Gene therapy for human skin disease produces long-term benefits

(Cell Press) In a study publishing in the journal Stem Cell Reports, researchers evaluated a patient with a genetic skin disorder known as epidermolysis bullosa nearly seven years after he had undergone a gene therapy procedure as part of a clinical trial. The study revealed that a small number of skin stem cells transplanted into the patient's legs were sufficient to restore normal skin function, without causing any adverse side effects.
Source: EurekAlert! - Medicine and Health - Category: Global & Universal Source Type: news