Sustained FXN expression in dorsal root ganglia from a nonreplicative genomic HSV ‐1 vector

ConclusionsOur results support the feasibility of using this vector for sustained neuronal expression of human frataxin for FA gene therapy.

Source: The Journal of Gene Medicine - August 1, 2017 Category: Genetics & Stem Cells Authors: Maria Ventosa, Zetang Wu, Filip Lim Tags: RESEARCH ARTICLE Source Type: research