The Muscular Dystrophy Association (MDA) U.S. Neuromuscular Disease (NMD) Registry: Initial Data on Patients with Spinal Muscular Atrophy (SMA) (P4.148)

Conclusions:The generalizability of SMA patients treated at MDA clinics to all SMA patients requires further exploration. The MDA Registry is one of the largest clinic-based observational longitudinal cohorts of SMA patients in the US and is a valuable resource to describe and characterize SMA and its comprehensive clinical care.Study Supported by: BiogenDisclosure: Dr. Jones has received personal compensation for activities withBiogen as an employee. Dr. Jones holds stock and/or stock options in Biogen. Dr. Eaton has received personal compensation for activities with Biogen as an employee. Dr. Eaton holds stock and/or stock options in Biogen. Dr. Li has received personal compensation for activities with Biogen as an employee. Dr. Li holds stock and/or stock options in Biogen, which sponsored research in which Dr. Li was involved as an investigator. Dr. Wang has received personal compensation for activities with Biogen as a contractor. Dr. Cwik has nothing to disclose. Dr. Cook has received personal compensation for activities with Biogen as a contractor. Dr. Gheuens has received personal compensation for activities with Biogen as an employee. Dr. Dilley has received personal compensation for activities with Biogen as an employee. Dr. Dilley holds stock in Biogen.

Source: Neurology - April 17, 2017 Category: Neurology Authors: Jones, C. C., Eaton, S., Li, L., Wang, N., Cwik, V., Cook, S. F., Gheuens, S., Dilley, A. Tags: Child Neurology II Source Type: research