Intravitreal Delivery of PEGylated-ECO Plasmid DNA Nanoparticles for Gene Therapy of Stargardt Disease

ConclusionsIntravitreal delivery of the PEG-ELNP ofpGRK1-ABCA4-S/MAR is a promising approach for gene therapy of Stargardt Disease, which can also be a delivery platform for gene therapy of other inherited retinal diseases.

Source: Pharmaceutical Research - March 5, 2024 Category: Drugs & Pharmacology Source Type: research