Alnylam Presents New Positive Clinical Results for Givosiran, an Investigational RNAi Therapeutic for the Treatment of Acute Hepatic Porphyrias
CAMBRIDGE, Mass.--(BUSINESS WIRE)--Apr. 14, 2018-- Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), the leading RNAi therapeutics company, today announced new results from the Phase 1 and Phase 1/2 open-label extension (OLE) studies of givosiran, an... (Source: Drugs.com - Clinical Trials)
Source: Drugs.com - Clinical Trials - April 14, 2018 Category: Pharmaceuticals Source Type: clinical trials

ENVISION: A Study to Evaluate the Efficacy and Safety of Givosiran (ALN-AS1) in Patients With Acute Hepatic Porphyrias (AHP)
Conditions:   Acute Hepatic Porphyria;   Acute Intermittent Porphyria;   Porphyria, Acute Intermittent;   Acute Porphyria;   Hereditary Coproporphyria (HCP);   Variegate Porphyria (VP);   ALA Dehydratase Deficient Porphyria (ADP) Interventions:   Drug: Givosiran;   Drug: Placebo Sponsor:   Alnylam Pharmaceuticals Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - November 9, 2017 Category: Research Source Type: clinical trials