Panhematin for Prevention of Acute Attacks of Porphyria Panhematin for Prevention of Acute Attacks of Porphyria
Conditions: Acute Intermittent Porphyria; Hereditary Coproporphyria; Variegate Porphyria Interventions: Biological: Hemin for injection; Other: Placebo Sponsor: The University of Texas Medical Branch, Galveston Recruiting - verified September 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 1, 2016 Category: Research Source Type: clinical trials
A Phase 1 Study of ALN-AS1 in Patients With Acute Intermittent Porphyria (AIP)
Condition: Acute Intermittent PorphyriaInterventions: Drug: ALN-AS1; Drug: Sterile Normal Saline (0.9% NaCl)Sponsor: Alnylam PharmaceuticalsRecruiting - verified May 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - May 19, 2015 Category: Research Source Type: clinical trials
EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition: Acute Hepatic PorphyriaIntervention: Sponsor: Alnylam PharmaceuticalsRecruiting - verified September 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 15, 2014 Category: Research Source Type: clinical trials
EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition: Acute Hepatic PorphyriaIntervention: Sponsor: Alnylam PharmaceuticalsRecruiting - verified February 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 11, 2014 Category: Research Source Type: clinical trials