EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition: Acute Hepatic PorphyriaIntervention: Sponsor: Alnylam PharmaceuticalsRecruiting - verified September 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 11, 2014 Category: Research Source Type: clinical trials
EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition: Acute Hepatic PorphyriaIntervention: Sponsor: Alnylam PharmaceuticalsRecruiting - verified May 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 11, 2014 Category: Research Source Type: clinical trials
Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria
Condition: Acute PorphyriasInterventions: Biological: Panhematin; Other: PlaceboSponsor: The University of Texas, GalvestonRecruiting - verified January 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 25, 2014 Category: Research Source Type: clinical trials
Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria
Condition: Acute Intermittent PorphyriaInterventions: Genetic: rAAV2/5-PBGD vector dosage 1; Genetic: rAAV2/5-PBGD vector dosage 2; Genetic: rAAV2/5-PBGD vector dosage 3; Genetic: rAAV2/5-PBGD vector dosage 4Sponsors: Digna Biotech S.L.; Porphyria Centre Sweden; Centro de Investigacion Medica Aplicada de Navarra; UniQure N. V.; Nationales Centrum für TumorerkrankungenCompleted - verified December 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 28, 2014 Category: Research Source Type: clinical trials
Mitoferrin-1 Expression in Erythropoietic Protoporphyria (Porphyria Rare Disease Clinical Research Consortium (RDCRC))
Condition: Erythropoietic Protoporphyria (EPP)Intervention: Sponsors: University of Alabama at Birmingham; Porphyria Rare Disease Clinical Research ConsortiumRecruiting - verified March 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 17, 2013 Category: Research Source Type: clinical trials