EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition:   Acute Hepatic PorphyriaIntervention:   Sponsor:   Alnylam PharmaceuticalsRecruiting - verified September 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 11, 2014 Category: Research Source Type: clinical trials

EXPLORE: A Natural History Study of Acute Hepatic Porphyria (AHP)
Condition:   Acute Hepatic PorphyriaIntervention:   Sponsor:   Alnylam PharmaceuticalsRecruiting - verified May 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - September 11, 2014 Category: Research Source Type: clinical trials

Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria
Condition:   Acute PorphyriasInterventions:   Biological: Panhematin;   Other: PlaceboSponsor:   The University of Texas, GalvestonRecruiting - verified January 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 25, 2014 Category: Research Source Type: clinical trials

Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria
Condition:   Acute Intermittent PorphyriaInterventions:   Genetic: rAAV2/5-PBGD vector dosage 1;   Genetic: rAAV2/5-PBGD vector dosage 2;   Genetic: rAAV2/5-PBGD vector dosage 3;   Genetic: rAAV2/5-PBGD vector dosage 4Sponsors:   Digna Biotech S.L.;   Porphyria Centre Sweden;   Centro de Investigacion Medica Aplicada de Navarra;   UniQure N. V.;   Nationales Centrum für TumorerkrankungenCompleted - verified December 2014 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 28, 2014 Category: Research Source Type: clinical trials

Mitoferrin-1 Expression in Erythropoietic Protoporphyria (Porphyria Rare Disease Clinical Research Consortium (RDCRC))
Condition:   Erythropoietic Protoporphyria (EPP)Intervention:   Sponsors:   University of Alabama at Birmingham;   Porphyria Rare Disease Clinical Research ConsortiumRecruiting - verified March 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 17, 2013 Category: Research Source Type: clinical trials