A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials

Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy and Metachromatic Leukodystrophy
Conditions:   Adrenoleukodystrophy;   Adrenomyeloneuropathy;   Metachromatic Leukodystrophy Intervention:   Diagnostic Test: Blood sample collection Sponsor:   Assistance Publique - Hôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 14, 2021 Category: Research Source Type: clinical trials