A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 10, 2021 Category: Research Source Type: clinical trials
Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy and Metachromatic Leukodystrophy
Conditions: Adrenoleukodystrophy; Adrenomyeloneuropathy; Metachromatic Leukodystrophy Intervention: Diagnostic Test: Blood sample collection Sponsor: Assistance Publique - Hôpitaux de Paris Not yet recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - June 14, 2021 Category: Research Source Type: clinical trials