New Diagnostic and Therapeutic Approaches in Leukodystrophy
Conditions: White Matter Diseases; LeukodystrophyInterventions: Other: Whole Genome Sequencing (WGS); Other: Standard Clinical Care and Diagnostic ApproachesSponsors: Children's Research Institute; Illumina, Inc.Recruiting - verified March 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 16, 2016 Category: Research Source Type: clinical trials
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
Conditions: Metachromatic Leukodystrophy; AdrenoleukodystrophyIntervention: Genetic: transduced CD34+ hematopoietic stem cellSponsors: Shenzhen Second People's Hospital; Shenzhen University; Guangzhou Women and Children's Medical CenterRecruiting - verified September 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 12, 2015 Category: Research Source Type: clinical trials