New Diagnostic and Therapeutic Approaches in Leukodystrophy
Conditions:   White Matter Diseases;   LeukodystrophyInterventions:   Other: Whole Genome Sequencing (WGS);   Other: Standard Clinical Care and Diagnostic ApproachesSponsors:   Children's Research Institute;   Illumina, Inc.Recruiting - verified March 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - February 16, 2016 Category: Research Source Type: clinical trials

Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
Conditions:   Metachromatic Leukodystrophy;   AdrenoleukodystrophyIntervention:   Genetic: transduced CD34+ hematopoietic stem cellSponsors:   Shenzhen Second People's Hospital;   Shenzhen University;   Guangzhou Women and Children's Medical CenterRecruiting - verified September 2015 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 12, 2015 Category: Research Source Type: clinical trials