Natural History of the Leukodystrophies
Condition: Leukodystrophies Intervention: Sponsor: Baylor Research Institute Recruiting - verified July 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - April 7, 2016 Category: Research Source Type: clinical trials
Safety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)
Condition: Hurler Syndrome, Metachromatic Leukodystrophy (MLD), Globoid Cell Leukodystrophy (Krabbe) and Cerebral Adrenoleukodystrophy (cALD)Intervention: Drug: Umbilical cord blood transplantation with HSC835Sponsor: Novartis PharmaceuticalsNot yet recruiting - verified March 2016 (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - March 16, 2016 Category: Research Source Type: clinical trials