BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions: Hurler Syndrome; Inherited Metabolic Disorder; Lysosomal Storage Disorder; Metachromatic Leukodystrophy; Inborn Errors of Metabolism Interventions: Biological: rivogenlecleucel; Drug: rimiducid Sponsor: Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition: Leukodystrophy Intervention: Sponsor: University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions: Hurler Syndrome; Inherited Metabolic Disorder; Lysosomal Storage Disorder; Metachromatic Leukodystrophy; Inborn Errors of Metabolism Interventions: Biological: rivogenlecleucel; Drug: rimiducid Sponsor: Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition: Leukodystrophy Intervention: Sponsor: University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions: Hurler Syndrome; Inherited Metabolic Disorder; Lysosomal Storage Disorder; Metachromatic Leukodystrophy; Inborn Errors of Metabolism Interventions: Biological: rivogenlecleucel; Drug: rimiducid Sponsor: Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition: Leukodystrophy Intervention: Sponsor: University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions: Hurler Syndrome; Inherited Metabolic Disorder; Lysosomal Storage Disorder; Metachromatic Leukodystrophy; Inborn Errors of Metabolism Interventions: Biological: rivogenlecleucel; Drug: rimiducid Sponsor: Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials
A Safety and Efficacy Study of Cryopreserved GSK2696274 for Treatment of Metachromatic Leukodystrophy (MLD)
Condition: Lysosomal Storage Disease Intervention: Drug: GSK2696274 Sponsors: GlaxoSmithKline; Ospedale (Hospital) San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 8, 2018 Category: Research Source Type: clinical trials