BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions:   Hurler Syndrome;   Inherited Metabolic Disorder;   Lysosomal Storage Disorder;   Metachromatic Leukodystrophy;   Inborn Errors of Metabolism Interventions:   Biological: rivogenlecleucel;   Drug: rimiducid Sponsor:   Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition:   Leukodystrophy Intervention:   Sponsor:   University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions:   Hurler Syndrome;   Inherited Metabolic Disorder;   Lysosomal Storage Disorder;   Metachromatic Leukodystrophy;   Inborn Errors of Metabolism Interventions:   Biological: rivogenlecleucel;   Drug: rimiducid Sponsor:   Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition:   Leukodystrophy Intervention:   Sponsor:   University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions:   Hurler Syndrome;   Inherited Metabolic Disorder;   Lysosomal Storage Disorder;   Metachromatic Leukodystrophy;   Inborn Errors of Metabolism Interventions:   Biological: rivogenlecleucel;   Drug: rimiducid Sponsor:   Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

Natural History, Diagnosis, and Outcomes for Leukodystrophies
Condition:   Leukodystrophy Intervention:   Sponsor:   University of Utah Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligible for BPU004 Study
Conditions:   Hurler Syndrome;   Inherited Metabolic Disorder;   Lysosomal Storage Disorder;   Metachromatic Leukodystrophy;   Inborn Errors of Metabolism Interventions:   Biological: rivogenlecleucel;   Drug: rimiducid Sponsor:   Bellicum Pharmaceuticals Available (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - August 21, 2018 Category: Research Source Type: clinical trials

A Safety and Efficacy Study of Cryopreserved GSK2696274 for Treatment of Metachromatic Leukodystrophy (MLD)
Condition:   Lysosomal Storage Disease Intervention:   Drug: GSK2696274 Sponsors:   GlaxoSmithKline;   Ospedale (Hospital) San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Recruiting (Source: ClinicalTrials.gov)
Source: ClinicalTrials.gov - January 8, 2018 Category: Research Source Type: clinical trials