A Study of AAV9 Gene Therapy in Participants With Canavan Disease

Conditions:   Canavan Disease;   Demyelinating Diseases;   Genetic Diseases, Inborn;   Metabolism, Inborn Errors;   Metabolic Disease;   Neurological Diseases or Conditions;   Leukodystrophy;   Leukoencephalopathies;   Neurodevelopmental Disorders;   Neurodegenerative Diseases Intervention:   Biological: AAV9 BBP-812 Sponsor:   Aspa Therapeutics Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials