A Study of AAV9 Gene Therapy in Participants With Canavan Disease
Conditions: Canavan Disease; Demyelinating Diseases; Genetic Diseases, Inborn; Metabolism, Inborn Errors; Metabolic Disease; Neurological Diseases or Conditions; Leukodystrophy; Leukoencephalopathies; Neurodevelopmental Disorders; Neurodegenerative Diseases Intervention: Biological: AAV9 BBP-812 Sponsor: Aspa Therapeutics Not yet recruiting
Source: ClinicalTrials.gov - Category: Research Source Type: clinical trials