< a href= " /news-events/nih-research-matters/gene-therapy-restores-missing-enzyme-rare-childhood-disease " > Gene therapy restores missing enzyme in rare childhood disease < /a >

A small study found that gene therapy delivered into the brain was safe and beneficial in treating a debilitating neurological disease.
Source: NIH Research Matters from the National Institutes of Health (NIH) - Category: Consumer Health News Source Type: news