Long‐term outcome of enzyme‐replacement therapy in advanced Fabry disease: evidence for disease progression towards serious complications
ConclusionDespite ERT, clinically meaningful events including sudden cardiac death continue to develop in patients with advanced Fabry disease.This article is protected by copyright. All rights reserved.
Source: Journal of Internal Medicine - Category: Internal Medicine Authors: Frank Weidemann, Markus Niemann, Stefan Störk, Frank Breunig, Meinrad Beer, Claudia Sommer, Sebastian Herrmann, Georg Ertl, Christoph Wanner Tags: Original Article Source Type: research
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